Gene dosage-dependent rescue of HSP neurite defects in SPG4 patients' neurons
基因剂量依赖性挽救 SPG4 患者神经元中的 HSP 神经突缺陷
期刊:Human Molecular Genetics
影响因子:3.1
doi:10.1093/hmg/ddt644
Steven Havlicek, Zacharias Kohl, Himanshu K Mishra, Iryna Prots, Esther Eberhardt, Naime Denguir, Holger Wend, Sonja Plötz, Leah Boyer, Maria C N Marchetto, Stefan Aigner, Heinrich Sticht, Teja W Groemer, Ute Hehr, Angelika Lampert, Ursula Schlötzer-Schrehardt, Jürgen Winkler, Fred H Gage, Beate Win