日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Small molecule-directed differentiation of submerged-cultured human nasal airway epithelia for respiratory disease modeling

利用小分子定向分化浸没培养的人鼻气道上皮细胞用于呼吸系统疾病建模

Dreyer, Henriette H M; Ithakisiou, Georgia-Nefeli; Spelier, Sacha; Iwanski, Malina K; Katrukha, Eugene; Terstappen, Jonne; Rodenburg, Lisa W; Shekhar, Aditi; den Hertog-Oosterhoff, Loes A; Smits, Shannon M A; van der Windt, Isabelle S; Azink, Lotte T; Bijlard, Linda H M; Passier, Koen; van Beuningen, Sam F B; Lebbink, Robert Jan; Haarman, Eric G; van der Ent, Cornelis K; Kapitein, Lukas C; Bont, Louis J; Beekman, Jeffrey M; Amatngalim, Gimano D

Functional, Cohort-Level Assessment of CFTR Modulator Responses Using Biobanked Nasal Epithelial Cells from Individuals with Cystic Fibrosis

利用囊性纤维化患者生物样本库中的鼻上皮细胞,对 CFTR 调节剂反应进行功能性、队列水平评估

Aalbers, Bente L; Amatngalim, Gimano D; Aarts, Ellen M; Rodenburg, Lisa W; den Hertog-Oosterhoff, Loes A; Heijerman, Harry G M; Beekman, Jeffrey M

Patient-Derived Intestinal Organoids in the Global Cystic Fibrosis Landscape

全球囊性纤维化领域中患者来源的肠道类器官

Kroes, Suzanne; Taylor-Cousar, Jennifer L; Zampoli, Marco; Karadag, Bülent; van der Ent, Cornelis K; de Winter-de Groot, Karin M; Beekman, Jeffrey M; Spelier, Sacha

ACE-tRNAs are a platform technology for suppressing nonsense mutations that cause cystic fibrosis.

ACE-tRNA 是一种用于抑制导致囊性纤维化的无义突变的平台技术

Ko Wooree, Porter Joseph J, Spelier Sacha, Sorensen Emily G, Bhatt Priyanka, Gabell Jeffrey T, van der Windt Isabelle, Couch Tyler, Coote Kevin, Mense Martin, Beekman Jeffrey M, Lueck John D

The response of rare CFTR mutations to specific modulator combinations

罕见CFTR突变对特定调节剂组合的反应

Stanleigh, Noemie; Gur, Michal; Shteinberg, Michal; Weiss, Aryeh; Sebbag-Sznajder, Naama; Duran, Deborah; Grunewald, Myriam; Birimberg-Schwartz, Liron; Pevzner, Lea; Bar-Yoseph, Ronen; Beekman, Jeffrey M; Kerem, Eitan; Wilschanski, Michael; Kerem, Batsheva

The Promising Role of Intestinal Organoids in the Diagnostic Work-Up of Cystic Fibrosis Screen Positive Inconclusive Diagnosis/CFTR-Related Metabolic Syndrome (CFSPID/CRMS)

肠道类器官在囊性纤维化筛查阳性但诊断不确定/CFTR相关代谢综合征(CFSPID/CRMS)诊断工作中的潜在作用

Rodriguez Mier, Noelia; Destoop, Marlies; Spelier, Sacha; Ramalho, Anabela Santo; Beekman, Jeffrey M; Vermeulen, François; de Winter-de Groot, Karin M; Proesmans, Marijke

OrgaSegment: deep-learning based organoid segmentation to quantify CFTR dependent fluid secretion

OrgaSegment:基于深度学习的类器官分割方法,用于量化CFTR依赖性液体分泌

Lefferts, Juliet W; Kroes, Suzanne; Smith, Matthew B; Niemöller, Paul J; Nieuwenhuijze, Natascha D A; Sonneveld van Kooten, Heleen N; van der Ent, Cornelis K; Beekman, Jeffrey M; van Beuningen, Sam F B

Impaired SARS-CoV-2 specific T-cell response in patients with severe COVID-19

重症新冠肺炎患者体内SARS-CoV-2特异性T细胞反应受损

Rümke, Lidewij W; Smit, Wouter L; Bossink, Ailko; Limonard, Gijs J M; Muilwijk, Danya; Haas, Lenneke E M; Reusken, Chantal; van der Wal, Sanne; Thio, Bing J; van Os, Yvonne M G; Gremmels, Hendrik; Beekman, Jeffrey M; Nijhuis, Monique; Wensing, Annemarie M J; Heron, Michiel; Thijsen, Steven F T

CFTR Function Restoration upon Elexacaftor/Tezacaftor/Ivacaftor Treatment in Patient-Derived Intestinal Organoids with Rare CFTR Genotypes

在具有罕见CFTR基因型的患者来源肠道类器官中,Elexacaftor/Tezacaftor/Ivacaftor治疗可恢复CFTR功能

Lefferts, Juliet W; Bierlaagh, Marlou C; Kroes, Suzanne; Nieuwenhuijze, Natascha D A; Sonneveld van Kooten, Heleen N; Niemöller, Paul J; Verburg, Tibo F; Janssens, Hettie M; Muilwijk, Danya; van Beuningen, Sam F B; van der Ent, Cornelis K; Beekman, Jeffrey M

Forskolin-induced organoid swelling is associated with long-term cystic fibrosis disease progression

福斯克林诱导的类器官肿胀与囊性纤维化疾病的长期进展相关。

Muilwijk, Danya; de Poel, Eyleen; van Mourik, Peter; Suen, Sylvia W F; Vonk, Annelotte M; Brunsveld, Jesse E; Kruisselbrink, Evelien; Oppelaar, Hugo; Hagemeijer, Marne C; Berkers, Gitte; de Winter-de Groot, Karin M; Heida-Michel, Sabine; Jans, Stephan R; van Panhuis, Hannah; van der Eerden, Menno M; van der Meer, Renske; Roukema, Jolt; Dompeling, Edward; Weersink, Els J M; Koppelman, Gerard H; Vries, Robert; Zomer-van Ommen, Domenique D; Eijkemans, Marinus J C; van der Ent, Cornelis K; Beekman, Jeffrey M