Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency.
Sleeping Beauty mRNA-LNP 可在小鼠和 NHP 肝细胞中实现稳定的 rAAV 转基因表达,并提高载体效力
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.06.021
Zakas Philip M, Cunningham Sharon C, Doherty Ann, van Dijk Eva B, Ibraheim Raed, Yu Stephanie, Mekonnen Befikadu D, Lang Brendan, English Elizabeth J, Sun Gang, Duncan Miles C, Benczkowski Matthew S, Altshuler Robert C, Singh Malvenderjit Jagjit, Kibbler Emily S, Tonga Gulen Y, Wang Zi Jun, Wang Z Jane, Li Guangde, An Ding, Rottman James B, Bhavsar Yashvi, Purcell Cormac, Jain Rachit, Alberry Ryan, Roquet Nathaniel, Fu Yanfang, Citorik Robert J, Rubens Jacob R, Holmes Michael C, Cotta-Ramusino Cecilia, Querbes William, Alexander Ian E, Salomon William E