Multidisciplinary team meetings in treatment of spinal muscular atrophy adult patients: a real-life observatory for innovative treatments
多学科团队会议在脊髓性肌萎缩症成人患者治疗中的应用:创新疗法的真实案例观察
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-023-03008-6
Salort-Campana, Emmanuelle; Solé, Guilhem; Magot, Armelle; Tard, Céline; Noury, Jean-Baptiste; Behin, Anthony; De La Cruz, Elisa; Boyer, François; Lefeuvre, Claire; Masingue, Marion; Debergé, Louise; Finet, Armelle; Brison, Mélanie; Spinazzi, Marco; Pegat, Antoine; Sacconi, Sabrina; Malfatti, Edoardo; Choumert, Ariane; Bellance, Rémi; Bedat-Millet, Anne-Laure; Feasson, Léonard; Vuillerot, Carole; Jacquin-Piques, Agnès; Michaud, Maud; Pereon, Yann; Stojkovic, Tanya; Laforêt, Pascal; Attarian, Shahram; Cintas, Pascal