日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Prenatal delivery of a therapeutic antisense oligonucleotide achieves broad biodistribution in the brain and ameliorates Angelman syndrome phenotype in mice

产前注射治疗性反义寡核苷酸可在小鼠大脑中实现广泛生物分布,并改善 Angelman 综合征表型

Maria T Clarke, Laura Remesal, Lea Lentz, Danielle J Tan, David Young, Slesha Thapa, Shalini R Namuduri, Beltran Borges, Georgia Kirn, Jasmine Valencia, Manuel E Lopez, Jan H Lui, Lawrence R Shiow, Scott Dindot, Saul Villeda, Stephan J Sanders, Tippi C MacKenzie

Prenatal AAV9-GFP administration in fetal lambs results in transduction of female germ cells and maternal exposure to virus

产前给羊羔注射 AAV9-GFP 可导致雌性生殖细胞的转导和母体接触病毒

Beltran Borges, Antonia Varthaliti, Marisa Schwab, Maria T Clarke, Christopher Pivetti, Nalin Gupta, Cathryn R Cadwell, Ghiabe Guibinga, Shirley Phillips, Tony Del Rio, Fatih Ozsolak, Denise Imai-Leonard, Lingling Kong, Diana J Laird, Akos Herzeg, Charlotte J Sumner, Tippi C MacKenzie