Antisense oligonucleotide therapy reduces seizures and extends life span in an SCN2A gain-of-function epilepsy model
反义寡核苷酸疗法可减少 SCN2A 功能获得性癫痫模型中的癫痫发作并延长寿命
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI152079
Melody Li, Nikola Jancovski, Paymaan Jafar-Nejad, Lisseth E Burbano, Ben Rollo, Kay Richards, Lisa Drew, Alicia Sedo, Jacqueline Heighway, Svenja Pachernegg, Armand Soriano, Linghan Jia, Todd Blackburn, Blaine Roberts, Alex Nemiroff, Kelley Dalby, Snezana Maljevic, Christopher A Reid, Frank Rigo, St