日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Loss of C9orf72 impacts the peripheral neuromuscular system via immune dysregulation and accelerates the progression of amyotrophic lateral sclerosis in SOD-1 mutant mice.

C9orf72 的缺失通过免疫失调影响周围神经肌肉系统,并加速 SOD-1 突变小鼠肌萎缩侧索硬化症的进展。

Sironi Francesca, Tortarolo Massimo, Mazzucchi Sabrina, Camporeale Laura, Freschi Mattia, Arcadipane Eliana, De Giovanetti Giulia, Kurosaki Mami, Terao Mineko, Parlanti Paola, Podini Paola, Gentile Francesco, Bonetto Valentina, Cappello Valentina, Riva Nilo, Quattrini Angelo, Bendotti Caterina

Protective role of Angiogenin in muscle regeneration in amyotrophic lateral sclerosis: Diagnostic and therapeutic implications

血管生成素在肌萎缩侧索硬化症肌肉再生中的保护作用:诊断和治疗意义

Fabbrizio, Paola; Baindoor, Sharada; Margotta, Cassandra; Su, Junyi; Morrissey, Elena P; Woods, Ina; Hogg, Marion C; Vianello, Sara; Venø, Morten T; Kjems, Jørgen; Sorarù, Gianni; Bendotti, Caterina; Prehn, Jochen H M; Nardo, Giovanni

Correction: Host genetics and gut microbiota influence lipid metabolism and inflammation: potential implications for ALS pathophysiology in SOD1G93A mice

更正:宿主遗传和肠道菌群影响脂质代谢和炎症:对SOD1G93A小鼠ALS病理生理学的潜在影响

Niccolai, Elena; Di Gloria, Leandro; Trolese, Maria Chiara; Fabbrizio, Paola; Baldi, Simone; Nannini, Giulia; Margotta, Cassandra; Nastasi, Claudia; Ramazzotti, Matteo; Bartolucci, Gianluca; Bendotti, Caterina; Nardo, Giovanni; Amedei, Amedeo

C9ORF72 Is Pivotal to Maintain a Proper Protein Homeostasis in Mouse Skeletal Muscle.

C9ORF72 在维持小鼠骨骼肌中适当的蛋白质稳态方面起着关键作用。

Sironi Francesca, Parlanti Paola, Margotta Cassandra, Cassarà Jessica, Bonetto Valentina, Bendotti Caterina, Tortarolo Massimo, Cappello Valentina

Sephin1 reduces TDP-43 cytoplasmic mislocalization and improves motor neuron survival in ALS models.

Sephin1 可减少 TDP-43 胞质错位,并改善 ALS 模型中的运动神经元存活率

Abgueguen Emmanuelle, Tortarolo Massimo, Rouviere Laura, Marcuzzo Stefania, Camporeale Laura, Henriques Alexandre, Pasetto Laura, Culley Georgia R, Bonetto Valentina, Marian Anca, Lejeune Beatrice L, Visbecq Anne, Lauria Giuseppe, Kabashi Edor, Callizot Noëlle, Bendotti Caterina, Miniou Pierre Y

Distinct fingerprints of tRNA-derived small non-coding RNA in animal models of neurodegeneration

神经退行性疾病动物模型中tRNA衍生的小非编码RNA的独特指纹图谱

Baindoor, Sharada; Gibriel, Hesham A Y; Venø, Morten T; Su, Junyi; Morrissey, Elena Perez; Jirström, Elisabeth; Woods, Ina; Kenny, Aidan; Alves, Mariana; Halang, Luise; Fabbrizio, Paola; Bilen, Maria; Engel, Tobias; Hogg, Marion C; Bendotti, Caterina; Nardo, Giovanni; Slack, Ruth S; Kjems, Jørgen; Prehn, Jochen H M

Effect of RNS60 in amyotrophic lateral sclerosis: a phase II multicentre, randomized, double-blind, placebo-controlled trial

RNS60治疗肌萎缩侧索硬化症的疗效:一项II期多中心、随机、双盲、安慰剂对照试验

Beghi, Ettore; Pupillo, Elisabetta; Bianchi, Elisa; Bonetto, Valentina; Luotti, Silvia; Pasetto, Laura; Bendotti, Caterina; Tortarolo, Massimo; Sironi, Francesca; Camporeale, Laura; Sherman, Alexander V; Paganoni, Sabrina; Scognamiglio, Ada; De Marchi, Fabiola; Bongioanni, Paolo; Del Carratore, Renata; Caponnetto, Claudia; Diamanti, Luca; Martinelli, Daniele; Calvo, Andrea; Filosto, Massimiliano; Padovani, Alessandro; Piccinelli, Stefano Cotti; Ricci, Claudia; Dalla Giacoma, Stefania; De Angelis, Nicoletta; Inghilleri, Maurizio; Spataro, Rossella; La Bella, Vincenzo; Logroscino, Giancarlo; Lunetta, Christian; Tarlarini, Claudia; Mandrioli, Jessica; Martinelli, Ilaria; Simonini, Cecilia; Zucchi, Elisabetta; Monsurrò, Maria Rosaria; Ricciardi, Dario; Trojsi, Francesca; Riva, Nilo; Filippi, Massimo; Simone, Isabella Laura; Sorarù, Gianni; Spera, Cristina; Florio, Lucia; Messina, Sonia; Russo, Massimo; Siciliano, Gabriele; Conte, Amelia; Saddi, Maria Valeria; Carboni, Nicola; Mazzini, Letizia

Correction: Immune-mediated myogenesis and acetylcholine receptor clustering promote a slow disease progression in ALS mouse models

更正:免疫介导的肌生成和乙酰胆碱受体聚集促进ALS小鼠模型中疾病进展缓慢

Margotta, Cassandra; Fabbrizio, Paola; Ceccanti, Marco; Cambieri, Chiara; Rufolo, Gabriele; D'Agostino, Jessica; Trolese, Maria Chiara; Cifelli, Pierangelo; Alfano, Veronica; Laurini, Christian; Scaricamazza, Silvia; Ferri, Alberto; Sorarù, Gianni; Palma, Eleonora; Inghilleri, Maurizio; Bendotti, Caterina; Nardo, Giovanni

The p97-Nploc4 ATPase complex plays a role in muscle atrophy during cancer and amyotrophic lateral sclerosis.

p97-Nploc4 ATPase 复合物在癌症和肌萎缩侧索硬化症引起的肌肉萎缩中发挥作用

Re Cecconi Andrea David, Barone Mara, Gaspari Simona, Tortarolo Massimo, Bendotti Caterina, Porcu Luca, Terribile Giulia, Piccirillo Rosanna

Interplay between immunity and amyotrophic lateral sclerosis: Clinical impact

免疫与肌萎缩侧索硬化症的相互作用:临床影响

De Marchi, Fabiola; Munitic, Ivana; Amedei, Amedeo; Berry, James D; Feldman, Eva L; Aronica, Eleonora; Nardo, Giovanni; Van Weehaeghe, Donatienne; Niccolai, Elena; Prtenjaca, Nikolina; Sakowski, Stacey A; Bendotti, Caterina; Mazzini, Letizia