Parkinson's disease motor symptoms rescue by CRISPRa-reprogramming astrocytes into GABAergic neurons
CRISPRa技术通过将星形胶质细胞重编程为GABA能神经元来缓解帕金森病运动症状
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.15252/emmm.202114797
Jessica Giehrl-Schwab # ,Florian Giesert # ,Benedict Rauser ,Chu Lan Lao ,Sina Hembach ,Sandrine Lefort ,Ignacio L Ibarra ,Christina Koupourtidou ,Malte Daniel Luecken ,Dong-Jiunn Jeffery Truong ,Judith Fischer-Sternjak ,Giacomo Masserdotti ,Nilima Prakash ,Jovica Ninkovic ,Sabine M Hölter ,Daniela M Vogt Weisenhorn ,Fabian J Theis ,Magdalena Götz ,Wolfgang Wurst