Whole brain delivery of an instability-prone Mecp2 transgene improves behavioral and molecular pathological defects in mouse models of Rett syndrome
向全脑输送易不稳定的 Mecp2 转基因可改善雷特综合征小鼠模型中的行为和分子病理缺陷
期刊:Elife
影响因子:6.4
doi:10.7554/eLife.52629
Mirko Luoni #, Serena Giannelli #, Marzia Tina Indrigo, Antonio Niro, Luca Massimino, Angelo Iannielli, Laura Passeri, Fabio Russo, Giuseppe Morabito, Piera Calamita, Silvia Gregori, Benjamin Deverman, Vania Broccoli