Neuronopathic Gaucher disease: dysregulated mRNAs and miRNAs in brain pathogenesis and effects of pharmacologic chaperone treatment in a mouse model
神经性戈谢病:小鼠模型中脑发病机制中失调的 mRNA 和 miRNA 以及药物伴侣治疗的影响
期刊:Human Molecular Genetics
影响因子:3.1
doi:10.1093/hmg/ddv404
Nupur Dasgupta, You-Hai Xu, Ronghua Li, Yanyan Peng, Manoj K Pandey, Stuart L Tinch, Benjamin Liou, Venette Inskeep, Wujuan Zhang, Kenneth D R Setchell, Mehdi Keddache, Gregory A Grabowski, Ying Sun