Protein Delivery of an Artificial Transcription Factor Restores Widespread Ube3a Expression in an Angelman Syndrome Mouse Brain
人工转录因子的蛋白质传递恢复了 Angelman 综合征小鼠脑中广泛的 Ube3a 表达
期刊:Molecular Therapy
影响因子:12.1
doi:10.1038/mt.2015.236
Barbara J Bailus, Benjamin Pyles, Michelle M McAlister, Henriette O'Geen, Sarah H Lockwood, Alexa N Adams, Jennifer Trang T Nguyen, Abigail Yu, Robert F Berman, David J Segal