A Multi-Centre Prospective Study of the Efficacy and Safety of Alglucosidase Alfa in Chinese Patients With Infantile-Onset Pompe Disease
一项多中心前瞻性研究评估了阿糖苷酶α治疗中国婴儿型庞贝病患者的疗效和安全性
期刊:Frontiers in Pharmacology
影响因子:4.8
doi:10.3389/fphar.2022.903488
Zhu, Diqi; Zhu, Jiacong; Qiu, Wenjuan; Wang, Benzhen; Liu, Lin; Yu, Xiaodan; Ou, Zhenheng; Shan, Guangsong; Wang, Jian; Li, Bin; Chen, Xiaokang; Liu, Cong; Li, Zipu; Fu, Lijun