日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Disease burden of ATTR amyloidosis based on the SF-36(®) health survey

基于SF-36®健康调查的ATTR淀粉样变性疾病负担

Sanchorawala, Vaishali; Greatsinger, Alexandra; Staron, Andrew; Berk, John L; Mendelson, Lisa M; Joshi, Tracy; J Burke, Natasha; Tabatabaeepour, Nadia; Smith, Jess; Signorovitch, James

Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy: A Randomized Clinical Trial With Open-Label Extension

帕替西兰治疗伴有多发性神经病变的遗传性转甲状腺素蛋白淀粉样变性五年结果:一项开放标签扩展的随机临床试验

Adams, David; Wixner, Jonas; Polydefkis, Michael; Berk, John L; Conceição, Isabel M; Dispenzieri, Angela; Peltier, Amanda; Ueda, Mitsuharu; Bender, Shaun; Capocelli, Kelley; Jay, Patrick Y; Yureneva, Elena; Obici, Laura

Changing Treatment Landscape in Transthyretin Cardiac Amyloidosis

转甲状腺素蛋白心脏淀粉样变性治疗格局的变化

Fontana, Marianna; Berk, John L; Drachman, Brian; Garcia-Pavia, Pablo; Hanna, Mazen; Lairez, Olivier; Witteles, Ronald

Correction: Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform

更正:在伴有多发性神经病的遗传性转甲状腺素蛋白介导的淀粉样变性患者中,从inotersen换用eplontersen:来自NEURO-TTRansform的分析

Conceição, Isabel; Berk, John L; Weiler, Markus; Kowacs, Pedro A; Dasgupta, Noel R; Khella, Sami; Chao, Chi-Chao; Attarian, Shahram; Kwoh, T Jesse; Jung, Shiangtung W; Chen, Jersey; Viney, Nicholas J; Yu, Rosie Z; Gertz, Morie; Masri, Ahmad; Cruz, Márcia Waddington; Coelho, Teresa

Estimating Meaningful Differences in Measures of Neuropathic Impairment, Health-Related Quality of Life, and Nutritional Status in Patients With Hereditary Transthyretin Amyloidosis

评估遗传性转甲状腺素蛋白淀粉样变性患者神经病理性损伤、健康相关生活质量和营养状况指标的显著差异

Folkvaljon, Folke; Gertz, Morie; Gillmore, Julian D; Khella, Sami; Masri, Ahmad; Maurer, Mathew S; Cruz, Márcia Waddington; Wixner, Jonas; Chen, Jersey; Reicher, Barry; Kwoh, Jesse; Yarlas, Aaron; Berk, John L

Benefits of Patisiran on Functional Capacity in ATTR Cardiac Amyloidosis: Post Hoc Analysis of APOLLO-B

帕替西兰对 ATTR 型心脏淀粉样变性患者功能能力的影响:APOLLO-B 研究的事后分析

Berk, John L; Lairez, Olivier; Schwartzmann, Pedro; Bender, Shaun; White, Matthew T; Jay, Patrick Y; Danese, David; Witteles, Ronald

Knowledge mapping and research trends of stem cell in wound healing: A bibliometric analysis

干细胞在伤口愈合中的知识图谱及研究趋势:文献计量分析

Siddiqi, Omar K; Mints, Yuliya Y; Berk, John L; Connors, Lawreen; Doros, Gheorghe; Gopal, Deepa M; Kataria, Shivangi; Lohrmann, Graham; Pipilas, Alexandra R; Ruberg, Frederick L; Sun, Nianzhe; Sun, Yu; Xing, Yixuan; Xu, Laiyu; Chen, Zijie; Qing, Liming; Wu, Panfeng; Tang, Juyu

Impact of Baseline Neuropathy Severity on Vutrisiran Treatment Response in the Phase 3 HELIOS-A Study

基线神经病变严重程度对 Vutrisiran 治疗反应的影响(HELIOS-A 3 期研究)

Luigetti, Marco; Quan, Dianna; Berk, John L; Conceição, Isabel; Misumi, Yohei; Chao, Chi-Chao; Bender, Shaun; Aldinc, Emre; Vest, John; Adams, David

Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis

帕替西兰治疗转甲状腺素蛋白心脏淀粉样变性患者

Maurer, Mathew S; Kale, Parag; Fontana, Marianna; Berk, John L; Grogan, Martha; Gustafsson, Finn; Hung, Rebecca R; Gottlieb, Robert L; Damy, Thibaud; González-Duarte, Alejandra; Sarswat, Nitasha; Sekijima, Yoshiki; Tahara, Nobuhiro; Taylor, Mark S; Kubanek, Milos; Donal, Erwan; Palecek, Tomas; Tsujita, Kenichi; Tang, W H Wilson; Yu, Wen-Chung; Obici, Laura; Simões, Marcus; Fernandes, Fábio; Poulsen, Steen Hvitfeldt; Diemberger, Igor; Perfetto, Federico; Solomon, Scott D; Di Carli, Marcelo; Badri, Prajakta; White, Matthew T; Chen, Jihong; Yureneva, Elena; Sweetser, Marianne T; Jay, Patrick Y; Garg, Pushkal P; Vest, John; Gillmore, Julian D

Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy

Eplontersen 用于治疗伴有多发性神经病变的遗传性转甲状腺素蛋白淀粉样变性

Coelho, Teresa; Marques, Wilson Jr; Dasgupta, Noel R; Chao, Chi-Chao; Parman, Yesim; França, Marcondes Cavalcante Jr; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R; Kowacs, Pedro A; Berk, John L; Obici, Laura; Barroso, Fabio A; Weiler, Markus; Conceição, Isabel; Jung, Shiangtung W; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G; Schneider, Eugene; Viney, Nicholas J; Masri, Ahmad; Gertz, Morie R; Ando, Yukio; Gillmore, Julian D; Khella, Sami; Dyck, P James B; Waddington Cruz, Márcia