日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Outcomes of hematopoietic stem cell gene therapy for Wiskott-Aldrich syndrome

造血干细胞基因治疗Wiskott-Aldrich综合征的疗效

Labrosse, Roxane; Chu, Julia I; Armant, Myriam A; Everett, John K; Pellin, Danilo; Kareddy, Niharika; Frelinger, Andrew L; Henderson, Lauren A; O'Connell, Amy E; Biswas, Amlan; Coenen-van der Spek, Jet; Miggelbrink, Alexandra; Fiorini, Claudia; Adhikari, Hriju; Berry, Charles C; Cantu, Vito Adrian; Fong, Johnson; Jaroslavsky, Jason; Karadeniz, Derin F; Li, Quan-Zhen; Reddy, Shantan; Roche, Aoife M; Zhu, Chengsong; Whangbo, Jennifer S; Dansereau, Colleen; Mackinnon, Brenda; Morris, Emily; Koo, Stephanie M; London, Wendy B; Baris, Safa; Ozen, Ahmet; Karakoc-Aydiner, Elif; Despotovic, Jenny M; Forbes Satter, Lisa R; Saitoh, Akihiko; Aizawa, Yuta; King, Alejandra; Nguyen, Mai Anh Thi; Vu, Vy Do Uyen; Snapper, Scott B; Galy, Anne; Notarangelo, Luigi D; Bushman, Frederic D; Williams, David A; Pai, Sung-Yun

INSPIIRED: Quantification and Visualization Tools for Analyzing Integration Site Distributions

INSPIIRED:用于分析整合位点分布的量化和可视化工具

Berry, Charles C; Nobles, Christopher; Six, Emmanuelle; Wu, Yinghua; Malani, Nirav; Sherman, Eric; Dryga, Anatoly; Everett, John K; Male, Frances; Bailey, Aubrey; Bittinger, Kyle; Drake, Mary J; Caccavelli, Laure; Bates, Paul; Hacein-Bey-Abina, Salima; Cavazzana, Marina; Bushman, Frederic D

INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes

INSPIIRED:用于定量分析细胞基因组中新DNA整合位点的流程

Sherman, Eric; Nobles, Christopher; Berry, Charles C; Six, Emmanuelle; Wu, Yinghua; Dryga, Anatoly; Malani, Nirav; Male, Frances; Reddy, Shantan; Bailey, Aubrey; Bittinger, Kyle; Everett, John K; Caccavelli, Laure; Drake, Mary J; Bates, Paul; Hacein-Bey-Abina, Salima; Cavazzana, Marina; Bushman, Frederic D

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

用于治疗X连锁重症联合免疫缺陷的改良型γ逆转录病毒载体

Hacein-Bey-Abina, Salima; Pai, Sung-Yun; Gaspar, H Bobby; Armant, Myriam; Berry, Charles C; Blanche, Stephane; Bleesing, Jack; Blondeau, Johanna; de Boer, Helen; Buckland, Karen F; Caccavelli, Laure; Cros, Guilhem; De Oliveira, Satiro; Fernández, Karen S; Guo, Dongjing; Harris, Chad E; Hopkins, Gregory; Lehmann, Leslie E; Lim, Annick; London, Wendy B; van der Loo, Johannes C M; Malani, Nirav; Male, Frances; Malik, Punam; Marinovic, M Angélica; McNicol, Anne-Marie; Moshous, Despina; Neven, Benedicte; Oleastro, Matías; Picard, Capucine; Ritz, Jerome; Rivat, Christine; Schambach, Axel; Shaw, Kit L; Sherman, Eric A; Silberstein, Leslie E; Six, Emmanuelle; Touzot, Fabien; Tsytsykova, Alla; Xu-Bayford, Jinhua; Baum, Christopher; Bushman, Frederic D; Fischer, Alain; Kohn, Donald B; Filipovich, Alexandra H; Notarangelo, Luigi D; Cavazzana, Marina; Williams, David A; Thrasher, Adrian J

Comparing DNA integration site clusters with scan statistics

将DNA整合位点簇与扫描统计数据进行比较

Berry, Charles C; Ocwieja, Karen E; Malani, Nirav; Bushman, Frederic D

HIV latency and integration site placement in five cell-based models

五种基于细胞的模型中HIV潜伏期和整合位点定位

Sherrill-Mix, Scott; Lewinski, Mary K; Famiglietti, Marylinda; Bosque, Alberto; Malani, Nirav; Ocwieja, Karen E; Berry, Charles C; Looney, David; Shan, Liang; Agosto, Luis M; Pace, Matthew J; Siliciano, Robert F; O'Doherty, Una; Guatelli, John; Planelles, Vicente; Bushman, Frederic D

Estimating abundances of retroviral insertion sites from DNA fragment length data

利用DNA片段长度数据估算逆转录病毒插入位点的丰度

Berry, Charles C; Gillet, Nicolas A; Melamed, Anat; Gormley, Niall; Bangham, Charles R M; Bushman, Frederic D

A method to sequence and quantify DNA integration for monitoring outcome in gene therapy

一种用于监测基因治疗结果的DNA整合测序和定量方法

Brady, Troy; Roth, Shoshannah L; Malani, Nirav; Wang, Gary P; Berry, Charles C; Leboulch, Philippe; Hacein-Bey-Abina, Salima; Cavazzana-Calvo, Marina; Papapetrou, Eirini P; Sadelain, Michel; Savilahti, Harri; Bushman, Frederic D

Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial

通过追踪逆转录病毒整合位点,分析人类 SCID-X1 基因治疗试验中基因修饰祖细胞的动态变化

Wang, Gary P; Berry, Charles C; Malani, Nirav; Leboulch, Philippe; Fischer, Alain; Hacein-Bey-Abina, Salima; Cavazzana-Calvo, Marina; Bushman, Frederic D

Analysis of lentiviral vector integration in HIV+ study subjects receiving autologous infusions of gene modified CD4+ T cells

对接受自体基因修饰CD4+ T细胞输注的HIV阳性研究对象进行慢病毒载体整合分析

Wang, Gary P; Levine, Bruce L; Binder, Gwendolyn K; Berry, Charles C; Malani, Nirav; McGarrity, Gary; Tebas, Pablo; June, Carl H; Bushman, Frederic D