日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: Huntington's disease cellular phenotypes are rescued non-cell autonomously by healthy cells in mosaic telencephalic organoids

作者更正:亨廷顿病细胞表型可通过嵌合型端脑类器官中的健康细胞以非细胞自主的方式得到挽救。

Galimberti, Maura; Nucera, Maria R; Bocchi, Vittoria D; Conforti, Paola; Vezzoli, Elena; Cereda, Matteo; Maffezzini, Camilla; Iennaco, Raffaele; Scolz, Andrea; Falqui, Andrea; Cordiglieri, Chiara; Cremona, Martina; Espuny-Camacho, Ira; Faedo, Andrea; Felsenfeld, Dan P; Vogt, Thomas F; Ranzani, Valeria; Zuccato, Chiara; Besusso, Dario; Cattaneo, Elena

Navigating triplet repeats sequencing: concepts, methodological challenges and perspective for Huntington's disease

三核苷酸重复序列测序:概念、方法学挑战及亨廷顿病研究展望

Maestri, Simone; Scalzo, Davide; Damaggio, Gianluca; Zobel, Martina; Besusso, Dario; Cattaneo, Elena

When repetita no-longer iuvant: somatic instability of the CAG triplet in Huntington's disease

当重复不再发生时:亨廷顿病中 CAG 三联体的体细胞不稳定性

Cattaneo, Elena; Scalzo, Davide; Zobel, Martina; Iennaco, Raffaele; Maffezzini, Camilla; Besusso, Dario; Maestri, Simone

A human CAGinSTEM platform for decoding HTT repeats' somatic instability links CAG interruption to HD pathology in neurons.

人类 CAGinSTEM 平台用于解码 HTT 重复序列的体细胞不稳定性,将 CAG 中断与神经元中的 HD 病理联系起来。

Zobel Martina, Damaggio Gianluca, Mignogna Maria Lidia, Besusso Dario, Scalzo Davide, Cossu Andrea, Trovesi Camilla, Crosti Mariacristina, Cortina Francesco, Campus Ilaria, Formenti Giulio, Mazzara Saveria, Gregoretti Francesco, Antonelli Laura, Oliva Gennaro, Zuccato Chiara, Colonna Vincenza, Conforti Paola, Cereda Matteo, Rossi Riccardo Lorenzo, Maestri Simone, Scolz Andrea, Iennaco Raffale, Cattaneo Elena

Huntington's disease cellular phenotypes are rescued non-cell autonomously by healthy cells in mosaic telencephalic organoids

亨廷顿病细胞表型可通过嵌合型端脑类器官中的健康细胞以非细胞自主的方式得到挽救。

Maura Galimberti ,Maria R Nucera ,Vittoria D Bocchi ,Paola Conforti ,Elena Vezzoli ,Matteo Cereda ,Camilla Maffezzini ,Raffaele Iennaco ,Andrea Scolz ,Andrea Falqui ,Chiara Cordiglieri ,Martina Cremona ,Ira Espuny-Camacho ,Andrea Faedo ,Dan P Felsenfeld ,Thomas F Vogt ,Valeria Ranzani ,Chiara Zuccato ,Dario Besusso ,Elena Cattaneo

Neuroprotection by ADAM10 inhibition requires TrkB signaling in the Huntington's disease hippocampus

通过抑制 ADAM10 实现神经保护需要亨廷顿病海马中的 TrkB 信号传导

Andrea Scolz, Elena Vezzoli, Michela Villa, Francesca Talpo, Jessica Cazzola, Francesca Raffin, Chiara Cordiglieri, Andrea Falqui, Giuseppe Pepe, Vittorio Maglione, Dario Besusso, Gerardo Biella, Chiara Zuccato

hESC-derived striatal progenitors grafted into a Huntington's disease rat model support long-term functional motor recovery by differentiating, self-organizing and connecting into the lesioned striatum

移植到亨廷顿氏病大鼠模型中的 hESC 衍生纹状体祖细胞可通过分化、自我组织和连接到受损纹状体来支持长期功能性运动恢复

Roberta Schellino #, Dario Besusso #, Roberta Parolisi, Gabriela B Gómez-González, Sveva Dallere, Linda Scaramuzza, Marta Ribodino, Ilaria Campus, Paola Conforti, Malin Parmar, Marina Boido, Elena Cattaneo #, Annalisa Buffo #

Modeling human telencephalic development and autism-associated SHANK3 deficiency using organoids generated from single neural rosettes

使用单个神经丛产生的类器官模拟人类端脑发育和自闭症相关的 SHANK3 缺陷

Yueqi Wang, Simone Chiola, Guang Yang, Chad Russell, Celeste J Armstrong, Yuanyuan Wu, Jay Spampanato, Paisley Tarboton, H M Arif Ullah, Nicolas U Edgar, Amelia N Chang, David A Harmin, Vittoria Dickinson Bocchi, Elena Vezzoli, Dario Besusso, Jun Cui, Elena Cattaneo, Jan Kubanek, Aleksandr Shcheglov

In vitro-derived medium spiny neurons recapitulate human striatal development and complexity at single-cell resolution

体外衍生的中棘神经元在单细胞分辨率下重现人类纹状体的发育和复杂性

Paola Conforti, Vittoria Dickinson Bocchi, Ilaria Campus, Linda Scaramuzza, Maura Galimberti, Tiziana Lischetti, Francesca Talpo, Matteo Pedrazzoli, Alessio Murgia, Ivan Ferrari, Chiara Cordiglieri, Alessandra Fasciani, Ernest Arenas, Dan Felsenfeld, Gerardo Biella, Dario Besusso, Elena Cattaneo

The coding and long noncoding single-cell atlas of the developing human fetal striatum

发育中的人类胎儿纹状体的编码和长非编码单细胞图谱

Vittoria Dickinson Bocchi, Paola Conforti, Elena Vezzoli, Dario Besusso, Claudio Cappadona, Tiziana Lischetti, Maura Galimberti, Valeria Ranzani, Raoul J P Bonnal, Marco De Simone, Grazisa Rossetti, Xiaoling He, Kenji Kamimoto, Ira Espuny-Camacho, Andrea Faedo, Federica Gervasoni, Romina Vuono, Sama