日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Inhaled DNAI1 mRNA therapy for treatment of primary ciliary dyskinesia.

吸入式 DNAI1 mRNA 疗法治疗原发性纤毛运动障碍

Hennig Mirko, Bhattacharjee Rumpa B, Agarwal Ishita, Alfaifi Ali, Casillas Jade E, Chavez Sofia, Ishimaru Daniella, Liston David, Mohapatra Sakya, Molla Touhidul, Pathare Suyog, Sidhu Maninder S, Wang Peng, Wang Zechen, Lombana T Noelle, Kharitonov Vladimir G, Couch Jessica A, Lockhart David J, Wustman Brandon A

Lipid nanoparticle-encapsulated Dnai1 mRNA rescues ciliary activity in primary ciliary dyskinesia mouse cell models

脂质纳米颗粒包裹的Dnai1 mRNA可挽救原发性纤毛运动障碍小鼠细胞模型中的纤毛活动。

Smith, Amanda J; Sears, Patrick R; Hennig, Mirko; Bhattacharjee, Rumpa B; Yin, Weining; Golliher, Hannah; Ishimaru, Daniella; Lombana, T Noelle; Lockhart, David J; Wustman, Brandon A; Ostrowski, Lawrence E