Prime editing-based gene correction alleviates the hyperexcitable phenotype and seizures of a genetic epilepsy mouse model
基于先导编辑的基因校正可缓解遗传性癫痫小鼠模型的过度兴奋表型和癫痫发作。
期刊:Acta Pharmacologica Sinica
影响因子:8.4
doi:10.1038/s41401-023-01115-5
Cao, Bi-Rong; Huang, Yi-Ming; Tian, Fu-Yun; Li, Jin-Hui; Xu, Chun-Long; Wei, Yu; Liu, Ji-Kai; Guo, Qian-Bei; Xu, Hai-Yan; Zhan, Li; Lv, Rui-Min; Sun, Yi-di; Hu, Xin-de; Gao, Zhao-Bing; Zhou, Chang-Yang