Prednisolone rescues Duchenne muscular dystrophy phenotypes in human pluripotent stem cell-derived skeletal muscle in vitro
泼尼松龙在体外挽救人类多能干细胞衍生骨骼肌中的杜氏肌营养不良症表型
期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:
doi:10.1073/pnas.2022960118
Ziad Al Tanoury, John F Zimmerman, Jyoti Rao, Daniel Sieiro, Harold M McNamara, Thomas Cherrier, Alejandra Rodríguez-delaRosa, Aurore Hick-Colin, Fanny Bousson, Charlotte Fugier-Schmucker, Fabio Marchiano, Bianca Habermann, Jérome Chal, Alexander P Nesmith, Svetlana Gapon, Erica Wagner, Vandana A Gu