日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma

ReNeu:一项针对有症状的1型神经纤维瘤病相关丛状神经纤维瘤成人和儿童的米达替尼关键性IIb期试验

Moertel, Christopher L; Hirbe, Angela C; Shuhaiber, Hans H; Bielamowicz, Kevin; Sidhu, Alpa; Viskochil, David; Weber, Michael D; Lokku, Armend; Smith, L Mary; Foreman, Nicholas K; Hajjar, Fouad M; McNall-Knapp, Rene Y; Weintraub, Lauren; Antony, Reuben; Franson, Andrea T; Meade, Julia; Schiff, David; Walbert, Tobias; Ambady, Prakash; Bota, Daniela A; Campen, Cynthia J; Kaur, Gurcharanjeet; Klesse, Laura J; Maraka, Stefania; Moots, Paul L; Nevel, Kathryn; Bornhorst, Miriam; Aguilar-Bonilla, Ana; Chagnon, Sarah; Dalvi, Nagma; Gupta, Punita; Khatib, Ziad; Metrock, Laura K; Nghiemphu, P Leia; Roberts, Ryan D; Robison, Nathan J; Sadighi, Zsila; Stapleton, Stacie; Babovic-Vuksanovic, Dusica; Gershon, Timothy R

Targeted Inhibition in Pediatric MET and ALK-Altered Hemispheric Gliomas: Objective Responses Followed by Treatment Resistance

儿童MET和ALK突变型半球胶质瘤的靶向抑制:客观缓解后出现治疗耐药

Wilson, David; Jayappa, Sateesh; Parker, Lora; Ocal, Eylem; Tanaka, Tomoko; Gokden, Murat; Bielamowicz, Kevin

A Phase I Study of Carfilzomib with Cyclophosphamide and Etoposide in Relapsed and Refractory Leukemia and Solid Tumors

卡非佐米联合环磷酰胺和依托泊苷治疗复发难治性白血病和实体瘤的I期研究

Boklan, Jessica; Langevin, Anne-Marie; Bielamowicz, Kevin; Neville, Kathleen; Trippett, Tanya; Brown, Valerie; DuBois, Steven G; Eshun, Francis; Gelfond, Jonathan; Zomet, Ativ; Narendran, Aru; Lacayo, Norman J

Prognostic Features of Recurrent Midline and H3 K27M-Mutant Glioma

复发性中线胶质瘤和H3 K27M突变型胶质瘤的预后特征

Bagley, Stephen J; Umemura, Yoshie; Mendez, Joe S; Arrillaga-Romany, Isabel; Bielamowicz, Kevin J; Butowski, Nick; Hutchins, Kelley; Kong, Xiao-Tang; Odia, Yazmin; Sharma, Akanksha; Weintraub, Lauren; Koschmann, Carl; Wen, Patrick Y; Saratsis, Amanda M; Brundage, Tom; Ramage, Samuel C; Tarapore, Rohinton S; Knowles, Truman; Yang, Dewen; Allen, Joshua E; Cloughesy, Timothy

A Checkpoint Reversal Receptor Mediates Bipartite Activation and Enhances CAR T-cell Function

检查点逆转受体介导双向激活并增强CAR T细胞功能

Daniel Landi # ,Shoba A Navai # ,Rebecca M Brock ,Kristen Fousek ,Zeid Nawas ,Khaled Sanber ,Cynthia Chauvin-Fleurence ,Raksha R Bhat ,Shuo Xu ,Purna Krishnamurthy ,Michelle Choe ,Matthew E Campbell ,Jessica S Morris ,Ahmed Z Gad ,Ankita Shree ,Alesandra S Echeandia Marrero ,Amr M Saadeldin ,Pretty R Matthew ,Dolores Mullikin ,Kevin Bielamowicz ,Lyazat Kurenbekova ,Angela M Major ,Vita S Salsman ,Tiara T Byrd ,John M Hicks ,Yi Jonathan Zhang ,Jason Yustein ,Alexandre F Carisey ,Sujith K Joseph ,Nabil Ahmed ,Meenakshi Hegde

Gut microbiota diversity is altered in a sex-dependent manner in Shank3B heterozygote mice

Shank3B杂合子小鼠的肠道菌群多样性以性别依赖的方式发生改变。

Turner, Finley; Williams, Mykle; Gregoretti, Sophie; Bielamowicz, Delano; Roach, Kylie; Gehner, Lil; Kunnatha, Anjali; Phillips, Shekinah; Hagel, Rosie; Harshman, Rebecca; Vargo, Erika; Dutton, Stacey B B; Kovacs, Jennifer; Larimore, Jennifer

Prospective External Validation of the Esbenshade Vanderbilt Models Accurately Predicts Bloodstream Infection Risk in Febrile Non-Neutropenic Children With Cancer

前瞻性外部验证表明,Esbenshade-Vanderbilt模型能够准确预测发热性非中性粒细胞减少症癌症患儿的血流感染风险。

Zhao, Zhiguo; Patel, Pratik A; Slatnick, Leonora; Sitthi-Amorn, Anna; Bielamowicz, Kevin J; Nunez, Farranaz A; Walsh, Alexandria M; Hess, Jennifer; Rossoff, Jenna; Elgarten, Caitlin; Myers, Regina; Saab, Raya; Basbous, Maya; Mccormick, Meghan; Aftandilian, Catherine; Richards, Rebecca; Nessle, C Nathan; Tribble, Alison C; Sheth Bhutada, Jessica K; Coven, Scott L; Runco, Daniel; Wilkes, Jennifer; Gurunathan, Arun; Guinipero, Terri; Belsky, Jennifer A; Lee, Karen; Wong, Victor; Malhotra, Megha; Armstrong, Amy; Jerkins, Lauren P; Cross, Shane J; Fisher, Lyndsay; Stein, Madison T; Wu, Natalie L; Yi, Troy; Orgel, Etan; Haeusler, Gabrielle M; Wolf, Joshua; Demedis, Jenna M; Miller, Tamara P; Esbenshade, Adam J

NFS-24. TUMOR VOLUME IN NEWLY DIAGNOSED OPTIC PATHWAY GLIOMAS ASSOCIATED WITH NF1 (NF1-OPG): PRELIMINARY RESULTS FROM THE INTERNATIONAL MULTICENTER NF1-OPG NATURAL HISTORY STUDY

NFS-24. 与NF1相关的视路胶质瘤(NF1-OPG)新诊断肿瘤体积:国际多中心NF1-OPG自然史研究的初步结果

O'Neill, Matthew J; Ng, Chai-Ann; Aizawa, Takanori; Sala, Luca; Bains, Sahej; Winbo, Annika; Ullah, Rizwan; Shen, Qianyi; Tan, Chek-Ying; Kozek, Krystian; Vanags, Loren R; Mitchell, Devyn W; Shen, Alex; Wada, Yuko; Kashiwa, Asami; Crotti, Lia; Dagradi, Federica; Musu, Giulia; Spazzolini, Carla; Neves, Raquel; Bos, J Martijn; Giudicessi, John R; Bledsoe, Xavier; Gamazon, Eric R; Lancaster, Megan; Glazer, Andrew M; Knollmann, Bjorn C; Roden, Dan M; Weile, Jochen; Roth, Frederick; Salem, Joe-Elie; Earle, Nikki; Stiles, Rachael; Agee, Taylor; Johnson, Christopher N; Horie, Minoru; Skinner, Jonathan; Ackerman, Michael J; Schwartz, Peter J; Ohno, Seiko; Vandenberg, Jamie I; Kroncke, Brett M; Fisher, Michael J; de Blank, Peter; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borcher, March; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; El-Dairi, Mays; Van Mater, David; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Oattes, Julius; Reddy, Alyssa; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Cutter, Gary; Avery, Robert; Levine, Adrian; Bennett, Julie; Li, Cyril; Rana, Mansuba; Yuditskiy, Richard; Ho, I-Chen; Haizel-Cobbina, Joseline; Hansford, Jordan; Luck, Amanda; Ludlow, Louise; Eisenstat, David; Toledano, Helen; Masoud, Roaya; Fukuoka, Kohei; Yamasaki, Kai; Nakano, Yoshiko; Mushtaq, Naureen; Minhas, Khurram; Bukhari, Syed Ibrahim; Stuecklin, Ana Guerreiro; Weiser, Annette; Jadrijevic-Cvilje, Filip; Fleming, Adam; Campbell, Shawde; Cacciotti, Chantel; Erker, Craig; van Landeghem, Frank; Wilson, Bev; Black, Karina; MacNeil, Mary; Cheng, Sylvia; Dunham, Chris; Larouche, Valerie; Giannakouros, Panagiota; Fonseca, Adriana; Williamson, Lane; Plant-Fox, Ashley; Levy, Jean Mulcahy; DeMarsh, Samantha; Vega, José Velázquez; Patil, Prabhumallikarjun; Nasrallah, MacLean; Santi-Vicini, Mariarita; Nelson, Ernest; Graham, Richard; Raskin, Scott; Fernandes, Igor; Dewan, Michael; Tabori, Uri; Hawkins, Cynthia; Senapati, Akanksha; Lindsay, Holly; Gilheeney, Stephen; Bale, Tejus; Taylor, Michael; Khuong-Quang, Dong-Anh; Bouffet, Eric; Khan, Sara; van Veelan, Marie-Lise; Kros, Johan M; Vasiljevic, Alexandre; Pollack, Ian; Chambless, Lola; Gupta, Nalin; Weiss, William A; Jabado, Nada; Sterba, Jaroslav; Zapotocky, Michal; Hansford, Jordan R; Ramaswamy, Vijay; Mikkelsen, Margit; Li, Xiaoyu; Yu, Kaiwen; High, Anthony; Tran, Haiyan; Furtado, Larissa V; Leelatian, Nalin; Berry, Julia D; Mobley, Bret C; Dewan, Michael C; May, Adriana; Kofler, Julia; Foster, Jessica; Lazow, Margot; Boué, Daniel R; Qaddoumi, Ibrahim; Robinson, Giles W; Peng, Junmin; Moreira, Daniel C; Chiang, Jason; Avery, Robert; Jiang, Zhifan; Parida, Abhijeet; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; de Blank, Peter; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borchert, Mark; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; Van Mater, David; El-Diari, Mays; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Oattes, Julius; Reddy, Alyssa; Cutter, Gary; Linguraru, Marius; Fisher, Michael

Molecular-guided therapy for the treatment of patients with relapsed and refractory childhood cancers: a Beat Childhood Cancer Research Consortium trial

分子靶向治疗复发难治性儿童癌症患者:一项由“战胜儿童癌症研究联盟”开展的试验

Sholler, Giselle L Saulnier; Bergendahl, Genevieve; Lewis, Elizabeth C; Kraveka, Jacqueline; Ferguson, William; Nagulapally, Abhinav B; Dykema, Karl; Brown, Valerie I; Isakoff, Michael S; Junewick, Joseph; Mitchell, Deanna; Rawwas, Jawhar; Roberts, William; Eslin, Don; Oesterheld, Javier; Wada, Randal K; Pastakia, Devang; Harrod, Virginia; Ginn, Kevin; Saab, Raya; Bielamowicz, Kevin; Glover, Jason; Chang, Eugenia; Hanna, Gina K; Enriquez, Daniel; Izatt, Tyler; Halperin, Rebecca F; Moore, Abigail; Byron, Sara A; Hendricks, William P D; Trent, Jeffrey M

IMMU-13. TRANS-SPECIES STUDY OF IDH-MUTANT REPLICATION-REPAIR DEFICIENT HIGH-GRADE GLIOMAS (RRD-HGG) AND RESPONSE TO COMBINED TARGETED AND IMMUNOTHERAPY: AN IRRDC STUDY

IMMU-13. IDH突变型复制修复缺陷型高级别胶质瘤(RRD-HGG)的跨物种研究及其对靶向治疗和免疫治疗联合反应的疗效:一项IRRDC研究

Poggi, Alessandro; Pietra, Gabriella; Caruana, Ignazio; Mariotti, Francesca Romana; Azzarone, Bruno; Das, Anirban; Mazzoli, Vienna; Fernandez, Nicholas; Aamir, Zoya; Nunes, Nuno; O’Flaherty, Katharine; Friedman, Hope; Bielamowicz, Kevin; Abebe-Campino, Gadi; Caspi, Shani; Nyman, Per; Graham, Richard; Kim, John; Wilhelmsson, Mari; Jorgensen, Mette; Michaeli, Orli; Fernandez, Maria; Reddy, Alyssa; Llosa, Nicholas; Li, Amanda; Levin, Adrian; Stengs, Lucie; Negm, Logine; Bianchi, Vanessa; Edwards, Melissa; Ertl-Wagner, Birgit; Bennett, Julie; Dirks, Peter; Bouffet, Eric; Hawkins, Cynthia; Tabori, Uri