日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Impact of minimal residual disease on the outcome of hematopoietic stem cell transplantation for childhood acute lymphoblastic leukemia within the FORUM trial

FORUM试验中微小残留病灶对儿童急性淋巴细胞白血病造血干细胞移植疗效的影响

Balduzzi, Adriana; Glogova, Evgenia; Peters, Christina; Sedlacek, Petr; Dalle, Jean-Hugues; Locatelli, Franco; Meisel, Roland; Burkhardt, Birgit; Buechner, Jochen; Wachowiak, Jacek; Bierings, Marc; Staciuk, Raquel; Graphakos, Stelios; Güngör, Tayfun; Yesilipek, Akif; Svec, Peter; Palma, Julia; Krivan, Gergely; Diaz-de-Heredia, Cristina; Limido, Francesca; Ansari, Marc; Kalwak, Krzysztof; Bader, Peter; Ifversen, Marianne

Comparable outcomes of HSCT up-front and after failure of IST in pediatric aplastic anemia in recent years

近年来,儿童再生障碍性贫血患者接受造血干细胞移植(HSCT)治疗,无论是否先进行免疫抑制治疗(IST),其疗效均相当。

Andresen, Felicia; Yoshimi, Ayami; Bader, Peter; Bierings, Marc; Bod'ová, Ivana; Bordon, Victoria; Buechner, Jochen; Burkhardt, Birgit; Dworzak, Michael; Erlacher, Miriam; Kállay, Krisztián; Labarque, Veerle; Locatelli, Franco; Malone, Andrea; Masmas, Tania; Müller, Ingo; Nöllke, Peter; Schmugge, Markus; Pawelec, Katarzyna; Sedlacek, Petr; Sevilla, Julian; Smith, Owen; Stary, Jan; Niemeyer, Charlotte; Strahm, Brigitte

Allele-selective disruption of pathogenic VWF variants in type 2 von Willebrand disease using CRISPR/Cas9

利用 CRISPR/Cas9 技术对 2 型血管性血友病中的致病性 VWF 变异体进行等位基因选择性破坏

Bär, Isabel; Groten, Stijn A; Barraclough, Alastair; Bürgisser, Petra E; van Kwawegen, Calvin; Lenting, Peter J; van Moort, Iris; Eikenboom, Jeroen C J; Leebeek, Frank W G; Voorberg, Jan; van den Biggelaar, Maartje; Bierings, Ruben

A novel cause of type 1 von Willebrand disease: impaired exocytosis of Weibel-Palade bodies due to biallelic MADD variants

型血管性血友病的新病因:双等位基因 MADD 变异导致 Weibel-Palade 小体胞吐受损

Hordijk, Sophie; Groten, Stijn A; Bürgisser, Petra E; Laan, Sebastiaan N J; Korenke, Georg Christoph; Honzík, Tomáš; Beysen, Diane; Leebeek, Frank W G; Skehel, Paul A; van den Biggelaar, Maartje; Carter, Tom; Bierings, Ruben

DDAVP response and its determinants in bleeding disorders: a systematic review and meta-analysis

DDAVP 反应及其在出血性疾病中的决定因素:系统评价和荟萃分析

Laan, Sebastiaan; Del Castillo Alferez, Jessica; Cannegieter, Suzanne; Fijnvandraat, Karin; Kruip, Marieke; le Cessie, Saskia; Bierings, Ruben; Eikenboom, Jeroen; van Moort, Iris

Disease characteristics and outcomes of acute myeloid leukemia in germline RUNX1 deficiency (Familial Platelet Disorder with associated Myeloid Malignancy)

生殖系 RUNX1 缺陷(伴有髓系恶性肿瘤的家族性血小板疾病)急性髓系白血病的疾病特征和预后

Ernst, Martijn P T; Versluis, Jurjen; Valk, Peter J M; Bierings, Marc; Tamminga, Rienk Y J; Hooimeijer, Louise H; Döhner, Konstanze; Gresele, Paolo; Tawana, Kiran; Langemeijer, Saskia M C; Van der Reijden, Bert A; Podgornik, Helena; Sever, Matjaz; Tvedt, Tor H A; Vulliamy, Tom; Fitzgibbon, Jude; Dokal, Inderjeet; Baliakas, Panagiotis; Bastida, José M; Pohlkamp, Christian; Haferlach, Torsten; Larcher, Lise; Soulier, Jean; Schutgens, Roger E G; Freson, Kathleen; Duployez, Nicolas; Löwenberg, Bob; Ericson, Katrin; Cammenga, Jörg; Ripperger, Tim; Raaijmakers, Marc H G P

Who owns that blood? Recontacting donors with results from genetic testing after allogeneic hematopoietic cell transplantation

血液的归属权是谁?异基因造血干细胞移植后,如何通过基因检测结果重新联系捐献者

Belderbos, Mirjam E; Bierings, Marc; van Bergeijk, Noa; van Thiel, Ghislaine J W M

Increased Clonal Hematopoiesis in Long-term Survivors of Pediatric Hematopoietic Cell Transplantation

儿童造血细胞移植长期幸存者的克隆造血增加

Konradin F Müskens, Nienke Wieringa, Maaike G J M van Bergen, Joëll E Bense, Brigit M Te Pas, Anne P J de Pagter, Arjan C Lankester, Marc B Bierings, Donna S Neuberg, Saskia Haitjema, Leontien C M Kremer, Gerwin A Huls, Stefan Nierkens, Joop H Jansen, Caroline A Lindemans, Aniek O de Graaf, Mirjam E

Immunoglobulin prophylaxis prevents hospital admissions for fever in pediatric acute lymphoblastic leukemia: results of a multicenter randomized trial

免疫球蛋白预防可降低儿童急性淋巴细胞白血病患者因发热入院的风险:一项多中心随机试验的结果

Thus, Kirsten A; De Groot-Kruseman, Hester A; Winkler-Seinstra, Pauline; Fiocco, Marta; Segers, Heidi; Van den Bos, Cor; Van der Sluis, Inge M; Tissing, Wim J E; Veening, Margreet A; Zwaan, Christian Michel; Van Tilburg, Cornelis M; Pieters, Rob; Bierings, Marc

Donor cytomegalovirus serology impacts overall survival in children receiving first unrelated hematopoietic stem cell transplant for acute leukemia: European Society of Bone Marrow Transplantation Pediatric Diseases Working Party Study

供体巨细胞病毒血清学对接受首次无关造血干细胞移植治疗急性白血病的儿童的总体生存率有影响:欧洲骨髓移植学会儿科疾病工作组研究

Ince, Elif; Galimard, Jaques-Emmanuel; Ifversen, Marianne; Dalissier, Arnaud; Szmit, Zofia; Mirci-Danicar, Oana; Locatelli, Franco; Sedlacek, Petr; Styczynski, Jan; Dalle, Jean-Hugues; Renard, Cecile; Balduzzi, Adriana; Lankester, Arjan; Bierings, Marc; Fagioli, Franca; Kielsen, Katrine; Rialland, Fanny; Büchner, Jochen; Taskinen, Mervi; Wynn, Robert; Jubert, Charlotte; Michel, Gérard; Pichler, Herbert; Krivan, Gergely; Cesaro, Simone; Corbacioglu, Selim; Meisel, Roland; Kalwak, Krzysztof