CFTR Function Restoration upon Elexacaftor/Tezacaftor/Ivacaftor Treatment in Patient-Derived Intestinal Organoids with Rare CFTR Genotypes
在具有罕见CFTR基因型的患者来源肠道类器官中,Elexacaftor/Tezacaftor/Ivacaftor治疗可恢复CFTR功能
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms241914539
Lefferts, Juliet W; Bierlaagh, Marlou C; Kroes, Suzanne; Nieuwenhuijze, Natascha D A; Sonneveld van Kooten, Heleen N; Niemöller, Paul J; Verburg, Tibo F; Janssens, Hettie M; Muilwijk, Danya; van Beuningen, Sam F B; van der Ent, Cornelis K; Beekman, Jeffrey M