Customizable virus-like particles deliver CRISPR-Cas9 ribonucleoprotein for effective ocular neovascular and Huntington's disease gene therapy.
可定制的病毒样颗粒递送 CRISPR-Cas9 核糖核蛋白,用于有效的眼部新生血管和亨廷顿病基因治疗
期刊:Nature Nanotechnology
影响因子:34.9
doi:10.1038/s41565-024-01851-7
Ling Sikai, Zhang Xue, Dai Yao, Jiang Zhuofan, Zhou Xujiao, Lu Sicong, Qian Xiaoqing, Liu Jianping, Selfjord Niklas, Satir Tugce Munise, Lundin Anders, Touza Julia Liz, Firth Mike, Van Zuydam Natalie, Bilican Bilada, Akcakaya Pinar, Hong Jiaxu, Cai Yujia