日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Customizable virus-like particles deliver CRISPR-Cas9 ribonucleoprotein for effective ocular neovascular and Huntington's disease gene therapy.

可定制的病毒样颗粒递送 CRISPR-Cas9 核糖核蛋白,用于有效的眼部新生血管和亨廷顿病基因治疗

Ling Sikai, Zhang Xue, Dai Yao, Jiang Zhuofan, Zhou Xujiao, Lu Sicong, Qian Xiaoqing, Liu Jianping, Selfjord Niklas, Satir Tugce Munise, Lundin Anders, Touza Julia Liz, Firth Mike, Van Zuydam Natalie, Bilican Bilada, Akcakaya Pinar, Hong Jiaxu, Cai Yujia

VHL Gene Restoration Supports RCC Reprogramming to iPSCs but Does Not Ensure Line Stability.

VHL基因恢复支持RCC重编程为iPSC,但不能保证细胞系稳定性。

Lichner Zsuzsanna, Shamshirgaran Yasaman, Pieczonka Katarzyna, Jonebring Anna, Kibschull Mark, Shynlova Oksana, Meens Jalna, Kim Raymond H, Ailles Laurie, Bilican Bilada, Hicks Ryan, Rogers Ian M

Correction: Human iPSC and CRISPR targeted gene knock-in strategy for studying the somatic TIE2L914F mutation in endothelial cells

更正:利用人诱导多能干细胞和CRISPR靶向基因敲入策略研究内皮细胞中的体细胞TIE2L914F突变

Lazovic, Bojana; Nguyen, Hoang-Tuan; Ansarizadeh, Mohammadhassan; Wigge, Leif; Kohl, Franziska; Li, Songyuan; Carracedo, Miguel; Kettunen, Jere; Krimpenfort, Luc; Elgendy, Ramy; Richter, Kati; De Silva, Laknee; Bilican, Bilada; Singh, Prateek; Saxena, Pratik; Jakobsson, Lars; Hong, Xuechong; Eklund, Lauri; Hicks, Ryan

A proteogenomic view of Parkinson's disease causality and heterogeneity

从蛋白质基因组学角度探讨帕金森病的病因和异质性

Kaiser, Sergio; Zhang, Luqing; Mollenhauer, Brit; Jacob, Jaison; Longerich, Simonne; Del-Aguila, Jorge; Marcus, Jacob; Raghavan, Neha; Stone, David; Fagboyegun, Olumide; Galasko, Douglas; Dakna, Mohammed; Bilican, Bilada; Dovlatyan, Mary; Kostikova, Anna; Li, Jingyao; Peterson, Brant; Rotte, Michael; Sanz, Vinicius; Foroud, Tatiana; Hutten, Samantha J; Frasier, Mark; Iwaki, Hirotaka; Singleton, Andrew; Marek, Ken; Crawford, Karen; Elwood, Fiona; Messa, Mirko; Serrano-Fernandez, Pablo

Human genetics uncovers MAP3K15 as an obesity-independent therapeutic target for diabetes

人类遗传学发现MAP3K15是糖尿病的一种与肥胖无关的治疗靶点。

Nag, Abhishek; Dhindsa, Ryan S; Mitchell, Jonathan; Vasavda, Chirag; Harper, Andrew R; Vitsios, Dimitrios; Ahnmark, Andrea; Bilican, Bilada; Madeyski-Bengtson, Katja; Zarrouki, Bader; Zoghbi, Anthony W; Wang, Quanli; Smith, Katherine R; Alegre-Díaz, Jesus; Kuri-Morales, Pablo; Berumen, Jaime; Tapia-Conyer, Roberto; Emberson, Jonathan; Torres, Jason M; Collins, Rory; Smith, David M; Challis, Benjamin; Paul, Dirk S; Bohlooly-Y, Mohammad; Snowden, Mike; Baker, David; Fritsche-Danielson, Regina; Pangalos, Menelas N; Petrovski, Slavé

High yields of oligodendrocyte lineage cells from human embryonic stem cells at physiological oxygen tensions for evaluation of translational biology

在生理氧张力下从人胚胎干细胞中获得高产量的少突胶质细胞谱系细胞,用于转化生物学评估

Stacpoole, Sybil R L; Spitzer, Sonia; Bilican, Bilada; Compston, Alastair; Karadottir, Ragnhildur; Chandran, Siddharthan; Franklin, Robin J M

Mutant induced pluripotent stem cell lines recapitulate aspects of TDP-43 proteinopathies and reveal cell-specific vulnerability

突变诱导多能干细胞系重现了TDP-43蛋白病的部分特征,并揭示了细胞特异性脆弱性。

Bilican, Bilada; Serio, Andrea; Barmada, Sami J; Nishimura, Agnes Lumi; Sullivan, Gareth J; Carrasco, Monica; Phatnani, Hemali P; Puddifoot, Clare A; Story, David; Fletcher, Judy; Park, In-Hyun; Friedman, Brad A; Daley, George Q; Wyllie, David J A; Hardingham, Giles E; Wilmut, Ian; Finkbeiner, Steven; Maniatis, Tom; Shaw, Christopher E; Chandran, Siddharthan