日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

UCART19, a first-in-class allogeneic anti-CD19 chimeric antigen receptor T-cell therapy for adults with relapsed or refractory B-cell acute lymphoblastic leukaemia (CALM): a phase 1, dose-escalation trial

UCART19 是一种首创的同种异体抗 CD19 嵌合抗原受体 T 细胞疗法,用于治疗复发或难治性 B 细胞急性淋巴细胞白血病 (CALM) 成人患者:一项 1 期剂量递增试验

Benjamin, Reuben; Jain, Nitin; Maus, Marcela V; Boissel, Nicolas; Graham, Charlotte; Jozwik, Agnieszka; Yallop, Deborah; Konopleva, Marina; Frigault, Matthew J; Teshima, Takanori; Kato, Koji; Boucaud, Floriane; Balandraud, Svetlana; Gianella-Borradori, Athos; Binlich, Florence; Marchiq, Ibtissam; Dupouy, Sandra; Almena-Carrasco, Maria; Pannaux, Matthieu; Fouliard, Sylvain; Brissot, Eolia; Mohty, Mohamad

Genome-edited, donor-derived allogeneic anti-CD19 chimeric antigen receptor T cells in paediatric and adult B-cell acute lymphoblastic leukaemia: results of two phase 1 studies

基因编辑的供体来源异基因抗CD19嵌合抗原受体T细胞治疗儿童和成人B细胞急性淋巴细胞白血病:两项I期研究的结果

Benjamin, Reuben; Graham, Charlotte; Yallop, Deborah; Jozwik, Agnieszka; Mirci-Danicar, Oana C; Lucchini, Giovanna; Pinner, Danielle; Jain, Nitin; Kantarjian, Hagop; Boissel, Nicolas; Maus, Marcela V; Frigault, Matthew J; Baruchel, André; Mohty, Mohamad; Gianella-Borradori, Athos; Binlich, Florence; Balandraud, Svetlana; Vitry, Fabien; Thomas, Elisabeth; Philippe, Anne; Fouliard, Sylvain; Dupouy, Sandra; Marchiq, Ibtissam; Almena-Carrasco, Maria; Ferry, Nicolas; Arnould, Sylvain; Konto, Cyril; Veys, Paul; Qasim, Waseem

Paediatric Strategy Forum for medicinal product development for acute myeloid leukaemia in children and adolescents: ACCELERATE in collaboration with the European Medicines Agency with participation of the Food and Drug Administration

儿童和青少年急性髓系白血病药物研发儿科战略论坛:ACCELERATE,与欧洲药品管理局合作,并有美国食品药品监督管理局参与

Pearson, Andrew D J; Zwaan, C Michel; Kolb, E Anders; Karres, Dominik; Guillot, Julie; Kim, Su Young; Marshall, Lynley; Tasian, Sarah K; Smith, Malcolm; Cooper, Todd; Adamson, Peter C; Barry, Elly; Benettaib, Bouchra; Binlich, Florence; Borgman, Anne; Brivio, Erica; Capdeville, Renaud; Delgado, David; Faller, Douglas; Fogelstrand, Linda; Fraenkel, Paula Goodman; Hasle, Henrik; Heenen, Delphine; Kaspers, Gertjan; Kieran, Mark; Klusmann, Jan-Henning; Lesa, Giovanni; Ligas, Franca; Mappa, Silvia; Mohamed, Hesham; Moore, Andrew; Morris, Joan; Nottage, Kerri; Reinhardt, Dirk; Scobie, Nicole; Simko, Stephen; Winkler, Thomas; Norga, Koen; Reaman, Gregory; Vassal, Gilles

Panobinostat plus bortezomib and dexamethasone in previously treated multiple myeloma: outcomes by prior treatment

帕比司他联合硼替佐米和地塞米松治疗既往接受过治疗的多发性骨髓瘤:按既往治疗情况分析疗效

Richardson, Paul G; Hungria, Vânia T M; Yoon, Sung-Soo; Beksac, Meral; Dimopoulos, Meletios Athanasios; Elghandour, Ashraf; Jedrzejczak, Wieslaw W; Guenther, Andreas; Nakorn, Thanyaphong Na; Siritanaratkul, Noppadol; Schlossman, Robert L; Hou, Jian; Moreau, Philippe; Lonial, Sagar; Lee, Jae Hoon; Einsele, Hermann; Sopala, Monika; Bengoudifa, Bourras-Rezki; Corrado, Claudia; Binlich, Florence; San-Miguel, Jesús F

Panobinostat PK/PD profile in combination with bortezomib and dexamethasone in patients with relapsed and relapsed/refractory multiple myeloma

帕比司他联合硼替佐米和地塞米松治疗复发性和复发/难治性多发性骨髓瘤患者的药代动力学/药效学特征

Mu, Song; Kuroda, Yoshiaki; Shibayama, Hirohiko; Hino, Masayuki; Tajima, Takeshi; Corrado, Claudia; Lin, Rong; Waldron, Edward; Binlich, Florence; Suzuki, Kenshi