日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

European Cross-Sectional Survey of Current Care Practices for Duchenne Muscular Dystrophy Reveals Regional and Age-Dependent Differences

欧洲杜氏肌营养不良症当前护理实践横断面调查揭示了地区和年龄差异

Vry, Julia; Gramsch, Kathrin; Rodger, Sunil; Thompson, Rachel; Steffensen, Birgit F; Rahbek, Jes; Doerken, Sam; Tassoni, Adrian; Beytía, María de Los Angeles; Guergueltcheva, Velina; Chamova, Teodora; Tournev, Ivailo; Kostera-Pruszczyk, Anna; Kaminska, Anna; Lusakowska, Anna; Mrazova, Lenka; Pavlovska, Lenka; Strenkova, Jana; Vondráček, Petr; Garami, Marta; Karcagi, Veronika; Herczegfalvi, Ágnes; Bushby, Katherine; Lochmüller, Hanns; Kirschner, Janbernd

Effect of weight maintenance on symptoms of knee osteoarthritis in obese patients: a twelve-month randomized controlled trial

体重维持对肥胖患者膝骨关节炎症状的影响:一项为期十二个月的随机对照试验

Christensen, Robin; Henriksen, Marius; Leeds, Anthony R; Gudbergsen, Henrik; Christensen, Pia; Sørensen, Tina J; Bartels, Else M; Riecke, Birgit F; Aaboe, Jens; Frederiksen, Rikke; Boesen, Mikael; Lohmander, L Stefan; Astrup, Arne; Bliddal, Henning

Rasch analysis of clinical outcome measures in spinal muscular atrophy

脊髓性肌萎缩症临床结果指标的Rasch分析

Cano, Stefan J; Mayhew, Anna; Glanzman, Allan M; Krosschell, Kristin J; Swoboda, Kathryn J; Main, Marion; Steffensen, Birgit F; Bérard, Carole; Girardot, Françoise; Payan, Christine A M; Mercuri, Eugenio; Mazzone, Elena; Elsheikh, Bakri; Florence, Julaine; Hynan, Linda S; Iannaccone, Susan T; Nelson, Leslie L; Pandya, Shree; Rose, Michael; Scott, Charles; Sadjadi, Reza; Yore, Mackensie A; Joyce, Cynthia; Kissel, John T

Classification and coding of rare diseases: overview of where we stand, rationale, why it matters and what it can change

罕见病分类与编码:现状概述、理论依据、重要性及潜在变革

Aymé, Ségolène; Andersen, Terkel; Kremp, Odile; Dosquet, Patrice; Rath, Ana; Autti-Rämö, Ilona; Amaral, Margarida D; Rodger, Sunil; Steffensen, Birgit F; Lochmüller, Hanns; Rodwell, Charlotte; Aymé, Ségolène; Bushby, Kate; Huyard, Caroline; Dunoyer, M; Rollet, P; Simoens, Steven; Edfjäll, Catarina; Aartsma-Rus, Annemieke; Verschuuren, Jan JGM; Campion, Giles V; van Ommen, Gert-jan B; van Deutekom, Judith CT; Lind, Ane; Jensen, Lene; Holm, Birthe B; Houÿez, François; Bélorgey, Chantal; North, Arielle; Czondi, Etelka; Lipucci di Paola, Michele; Kirschner, Jan; Rodger, Sunil; Vry, Julia; Gramsch, Kathrin; Lochmüller, Hanns; Bushby, Kate; Giehl, Julia; Graessner, Holm; Riess, Olaf; Parkinson, Kay; Mertens, Pierre; Aujoulat, Isabelle; Young, Bridget; Salmon, Peter; Bushby, Kate; Abetz-Webb, Linda; Roos, Marco; Schultes, Erik A; Mons, Barend; Weinreich, Stephanie S; Vrinten, Charlotte; Verschuuren, Jan JGM; Uyl-de Groot, Carin A; Kuijpers, Marja R; Sterrenburg, Ellen; Scholten, Rob JPM; van Bezooijen, Cees FRM; Timmen, Marcel FTH; van Weely, Sonja; Cornel, Martina C; Garcia, Alain; Nourissier, Christel; Sireau, Nicolas T; De Ridder, Ri; DeRidder, R; Adriaens, C; Kleinermans, D; Mortier, M; Quanten, A; Arickx, F; Lind, Ane; Jensen, Lene; Holm, Birthe B; Hughes-Wilson, Wills; Cassiman, Jean-Jacques; Pierri, Paola; Hannigan, Steve; Sofia, Francesca; Bellagambi, Simona; Taruscio, Domenica; Gainotti, Sabina; Vittozzi, Luciano; Bianchi, Fabrizio; Ensini, Monica; Posada, Manuel; Vroom, Elizabeth; Héon-Klin, Véronique; Halbach, Alexandra; Schlangen, Miriam; Schnieders, Birgit; Pypops, Ulrike; Wong-Rieger, Durhane; Byrne, Paula C; Robinson, Peter N