Targeting CAG repeat RNAs reduces Huntington's disease phenotype independently of huntingtin levels
靶向 CAG 重复 RNA 可降低亨廷顿氏病表型,且与亨廷顿蛋白水平无关
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI83185
Laura Rué, Mónica Bañez-Coronel, Jordi Creus-Muncunill, Albert Giralt, Rafael Alcalá-Vida, Gartze Mentxaka, Birgit Kagerbauer, M Teresa Zomeño-Abellán, Zeus Aranda, Veronica Venturi, Esther Pérez-Navarro, Xavier Estivill, Eulàlia Martí