DG9 boosts PMO nuclear uptake and exon skipping to restore dystrophic muscle and cardiac function.
DG9 促进 PMO 核摄取和外显子跳跃，从而恢复营养不良的肌肉和心脏功能
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-59494-8
Shah Md Nur Ahad, Wilton-Clark Harry, Haque Farhia, Powell Brooklynn, Sutanto Laura Edellein, Maradiya Radha, Zhabyeyev Pavel, Roshmi Rohini Roy, Anwar Saeed, Aslesh Tejal, Lim Kenji Rowel Q, Maruyama Rika, Bigot Anne, Young Courtney S, Bittner Scott, Spencer Melissa J, Moulton Hong M, Oudit Gavin Y, Yokota Toshifumi
