日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Valproic Acid Improves Antisense-Mediated Exon-Skipping Efficacy in mdx Mice.

丙戊酸可提高 mdx 小鼠中反义介导的外显子跳跃效率

Phongsavanh Micky, Bizot Flavien, Saoudi Amel, Gastaldi Cecile, Le Coz Olivier, Tensorer Thomas, Brisebard Elise, Garcia Luis, Goyenvalle Aurélie

Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model

寡核苷酸增强化合物可提高三环DNA介导的Mdx小鼠模型外显子跳跃效率

Bizot, Flavien; Fayssoil, Abdallah; Gastaldi, Cécile; Irawan, Tabitha; Phongsavanh, Xaysongkhame; Mansart, Arnaud; Tensorer, Thomas; Brisebard, Elise; Garcia, Luis; Juliano, Rudolph L; Goyenvalle, Aurélie

Partial Restoration of Brain Dystrophin and Behavioral Deficits by Exon Skipping in the Muscular Dystrophy X-Linked (mdx) Mouse

通过外显子跳跃技术部分恢复X连锁肌营养不良症(mdx)小鼠的脑肌营养不良蛋白和行为缺陷

Zarrouki, Faouzi; Relizani, Karima; Bizot, Flavien; Tensorer, Thomas; Garcia, Luis; Vaillend, Cyrille; Goyenvalle, Aurélie