Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model
寡核苷酸增强化合物可提高三环DNA介导的Mdx小鼠模型外显子跳跃效率
期刊:Cells
影响因子:5.2
doi:10.3390/cells12050702
Bizot, Flavien; Fayssoil, Abdallah; Gastaldi, Cécile; Irawan, Tabitha; Phongsavanh, Xaysongkhame; Mansart, Arnaud; Tensorer, Thomas; Brisebard, Elise; Garcia, Luis; Juliano, Rudolph L; Goyenvalle, Aurélie