日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II期FIREFLY-1试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

The use of minor response, volumetric assessment, and growth rate kinetics as endpoints in grade 1-3 glioma clinical trials: a RANO perspective

在 1-3 级胶质瘤临床试验中,以轻微反应、体积评估和生长速率动力学作为终点指标:RANO 的视角

van den Bent, Martin J; Cloughesy, Timothy F; Ellingson, Benjamin M; Allen, Joshua E; Blackman, Samuel C; Kieran, Mark W; Tonn, Joerg C; Karschnia, Philipp; Wijnenga, Maarten; Pallud, Johan; Young, Robert J; Huang, Raymond Y; Mellinghoff, Ingo K; de Groot, John; van der Hoorn, Anouk; Youssef, Gilbert; Hervey-Jumper, Shawn L; Vogelbaum, Michael A; Chang, Susan M; Wen, Patrick Y

Preclinical Activity of the Type II RAF Inhibitor Tovorafenib in Tumor Models Harboring Either a BRAF Fusion or an NF1 Loss-of-Function Mutation.

II 型 RAF 抑制剂托沃拉非尼在携带 BRAF 融合或 NF1 功能丧失突变的肿瘤模型中的临床前活性

Rastogi Shubhra, Perino Samantha, Lal-Nag Madhu, Wang Yujin, Blackman Samuel C, Venetsanakos Eleni

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II期FIREFLY-1试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

II 型 RAF 抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II 期 FIREFLY-1 试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

LOGGIC/FIREFLY-2: a phase 3, randomized trial of tovorafenib vs. chemotherapy in pediatric and young adult patients with newly diagnosed low-grade glioma harboring an activating RAF alteration

LOGGIC/FIREFLY-2:一项针对携带激活型 RAF 改变的初诊低级别胶质瘤儿童和青少年患者的托沃拉非尼与化疗的 3 期随机试验

van Tilburg, Cornelis M; Kilburn, Lindsay B; Perreault, Sébastien; Schmidt, Rene; Azizi, Amedeo A; Cruz-Martínez, Ofelia; Zápotocký, Michal; Scheinemann, Katrin; Meeteren, Antoinette Y N Schouten-van; Sehested, Astrid; Opocher, Enrico; Driever, Pablo Hernáiz; Avula, Shivaram; Ziegler, David S; Capper, David; Koch, Arend; Sahm, Felix; Qiu, Jiaheng; Tsao, Li-Pen; Blackman, Samuel C; Manley, Peter; Milde, Till; Witt, Ruth; Jones, David T W; Hargrave, Darren; Witt, Olaf

ETMR-28. EVALUATING THERAPEUTIC APPROACHES IN EMBRYONAL TUMORS WITH PLAGL1 AND PLAGL2 AMPLIFICATION AND UNRAVELING MOLECULAR PARALLELS IN EPIGENETICALLY RELATED TUMORS WITH PLAG1-ALTERATIONS

ETMR-28. 评估PLAG1和PLAG2扩增的胚胎性肿瘤的治疗方法,并揭示PLAG1改变的表观遗传相关肿瘤的分子平行性

Thorne, Tyler J; Nelson, Chase T; Lisitano, Leonard S J; Higgins, Thomas F; Rothberg, David L; Haller, Justin M; Marchand, Lucas S; Kline, Cassie; Waanders, Angela J; Ziegler, David S; Kilburn, Lindsay B; Nysom, Karsten; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Larouche, Valérie; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Oren, Michal Yalon; Toledano, Helen; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Whipple, Nicholas S; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Wright, Karen D; Blackman, Samuel C; Qiu, Jiaheng; Podesta, Dolores; Walter, Ashley; Da Costa, Daniel; Manley, Peter; McLeod, Lisa; Landi, Daniel B; Keck, Michaela-Kristina; Tietze, Anna; Sievers, Philipp; Bison, Brigitte; Avula, Shivaram; Brandner, Sebastian; Cheesman, Edmund; Faure-Conter, Cécile; Fenouil, Tanguy; Figarella-Branger, Dominique; Gauchotte, Guillaume; Goebell, Einar; Gojo, Johannes; Haberler, Christine; Hakumäki, Juhana; Hayden, James T; Jabado, Nada; Korhonen, Laura S; Korshunov, Andrey; Koscielniak, Ewa; Kramm, Christof M; Kranendonk, Mariëtte E G; Lavarino, Cinzia; Lequin, Maarten; Loiseau, Hugues; Ludlow, Louise E; Maher, Ossama; Meyronet, David; Nyman, Per; Øra, Ingrid; Perwein, Thomas; Pesola, Jouni; Rauramaa, Tuomas; Reddingius, Roel; Samuel, David; Schouten-van Meeteren, Antoinette Y N; Schüller, Ulrich; Sexton-Oates, Alexandra; Solomon, David; Varlet, Pascale; Vasiljevic, Alexandre; von Kalle, Thekla; Wefers, Annika K; Wesseling, Pieter; White, Christine; Zamecnik, Josef; Zapotocky, Michal; von Hoff*, Katja; Jones*, David T W

NFS-03. MEDULLOBLASTOMA IN CHILDREN WITH FANCONI ANEMIA: ASSOCIATION WITH FA-D1/FA-N, SHH TYPE AND POOR SURVIVAL INDEPENDENT OF TREATMENT STRATEGIES

NFS-03. 范可尼贫血患儿髓母细胞瘤:与 FA-D1/FA-N、SHH 型及与治疗策略无关的低生存率相关

Chukwu, Wolu; Lee, Siyun; Crane, Alexander; Zhang, Shu; Webster, Sophie; Mittra, Ipsa; Imielinski, Marcin; Beroukhim, Rameen; Dubois, Frank; Dalin, Simona; Seelow, Dominik; Öz, Elif; Hardt, Annika; Kortmann, Rolf-Dieter; Schwarz, Rudolf; Timmermann, Beate; Bison, Brigitte; Warmuth-Metz, Monika; von Hoff, Katja; von Bueren, André O; Gerber, Nicolas U; Fleischhack, Gudrun; Pietsch, Torsten; Pfister, Stefan M; Sturm, Dominik; Mynarek, Martin; Rutkowski, Stefan; Obrecht-Sturm, Denise; Faria Andrade*, Augusto; Sigaud*, Romain; Puligandla*, Evan; Liu, Bridget; Karimi, Elham; Schmid, Simone; Selt, Florian; Driever, Pablo Hernáiz; Koch, Arend; Sahm, Felix; Sievers, Philipp; Pfister, Stefan M; Witt, Olaf; Jones, David T W; Capper, David; Walsh*, Logan; Jabado*, Nada; Milde*, Till; Ghasemi, David R; von Hoff, Katja; Obrecht-Sturm, Denise; Wenning, Janna; Mynarek, Martin; Gerber, Nicolas U; Benesch, Martin; Juhnke, Björn O; Bison, Brigitte; Warmuth-Metz, Monika; Timmermann, Beate; Faldum, Andreas; Fleischhack, Gudrun; Grotzer, Michael; Driever, Pablo Hernáiz; Beilken, Andreas; Ebinger, Martin; Graf, Norbert; Frühwald, Michael; Schmid, Irene; Koch, Arend; Bergmann, Markus; Hagel, Christian; Coras, Roland; Blümcke, Ingmar; Reifenberger, Guido; Felsberg, Jörg; Keyvani, Kathy; Harter, Patrick N; Prinz, Marco; Staszewski, Ori; Acker, Till; Brück, Wolfgang; Hartmann, Christian; von Deimling, Andreas; Sommer, Clemens; Hasselblatt, Martin; Riemenschneider, Markus J; Monoranu, Camelia-Maria; Rushing, Elisabeth; Kool, Marcel; Pfister, Stefan M; Schüller, Ulrich; Pietsch, Torsten; Kortmann, Rolf D; Kwiecien, Robert; Witt, Hendrik; Pajtler, Kristian W; Rutkowski, Stefan; Fruehwald, Michael C; Boros, Matej; Dahlum, Sonja; Bens, Susanne; Johann, Pascal D; Kachanov, Denis; Hauser, Peter; Kratz, Christian P; Hernaiz-Driever, Pablo; Eyrich, Matthias; Sumerauer, David; Milde, Till; Reinhard, Harald; van de Wetering, Marianne; Gil-da-Costa, Maria Joao; Elisabetta, Schiavello; Kerl, Kornelius; Furtwaengler, Rhoikos; Kordes, Uwe; Gerss, Joachim; Hasselblatt, Martin; Nysom, Karsten; Nemes, Karolina; Kline, Cassie; Waanders, Angela J; Ziegler, David S; Kilburn, Lindsay B; Nysom, Karsten; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Larouche, Valérie; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Oren, Michal Yalon; Toledano, Helen; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Whipple, Nicholas S; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Wright, Karen D; Blackman, Samuel C; Qiu, Jiaheng; Podesta, Dolores; Walter, Ashley; Da Costa, Daniel; Manley, Peter; McLeod, Lisa; Landi, Daniel B; Geisemeyer, Neal; Federico, Aniello; Sill, Martin; Rosenblum, Marc; Bale, Tejus; Mauermann, Monika; Schrimpf, Daniel; Johann, Pascal; Pickles, Jessica; Aldape, Kenneth; Tauziède-Espariat, Arnault; Hasselblatt, Martin; Sturm, Dominik; Tietze, Anna; von Deimling, Andreas; Sievers, Philipp; Sahm, Felix; Gojo, Johannes; von Hoff, Katja; Pfister, Stefan M; Kool, Marcel; Keck, Michaela-Kristina; Tietze, Anna; Sievers, Philipp; Bison, Brigitte; Avula, Shivaram; Brandner, Sebastian; Cheesman, Edmund; Faure-Conter, Cécile; Fenouil, Tanguy; Figarella-Branger, Dominique; Gauchotte, Guillaume; Goebell, Einar; Gojo, Johannes; Haberler, Christine; Hakumäki, Juhana; Hayden, James T; Jabado, Nada; Korhonen, Laura S; Korshunov, Andrey; Koscielniak, Ewa; Kramm, Christof M; Kranendonk, Mariëtte E G; Lavarino, Cinzia; Lequin, Maarten; Loiseau, Hugues; Ludlow, Louise E; Maher, Ossama; Meyronet, David; Nyman, Per; Øra, Ingrid; Perwein, Thomas; Pesola, Jouni; Rauramaa, Tuomas; Reddingius, Roel; Samuel, David; Schouten-van Meeteren, Antoinette Y N; Schüller, Ulrich; Sexton-Oates, Alexandra; Solomon, David; Varlet, Pascale; Vasiljevic, Alexandre; von Kalle, Thekla; Wefers, Annika K; Wesseling, Pieter; White, Christine; Zamecnik, Josef; Zapotocky, Michal; von Hoff*, Katja; Jones*, David T W; Stepien, Natalia; Senfter, Daniel; Freund, Julia; Machreich, Sarah; Bruckner, Katharina; Mager, Leah; Laemmerer, Anna; Jaunecker, Carola; Pirker, Christine; Lötsch-Gojo, Daniela; Mayr, Lisa; Hedrich, Cora; Lippolis, Maria Aliotti; Schned, Hannah; Köller, Clara; Kiesel, Barbara; Dorfer, Christian; Azizi, Amedeo A; Peyrl, Andreas; Schmook, Maria T; Euskirchen, Philipp; Pagès-Gallego, Marc; Vermeulen, Carlo; Tops, Bastiaan; Haberler, Christine; Müllauer, Leonhard; Madlener, Sibylle; Gojo, Johannes; Schned, Hannah; Haberler, Christine; Peyrl, Andreas; Azizi, Amedeo; Mayr, Lisa; Aistleitner, Barbara; von Hoff, Katja; Kool, Marcel; Kjaersgaard, Mimi; Trkova, Katerina; Andre, Nicolas; Lippolis, Maria Aliotti; Hedrich, Cora; Köller, Clara; Stepien, Natalia; Slavc, Irene; Gojo, Johannes; Traunwieser, Thomas; Loos, Elena; Ottensmeier, Holger; Mynarek, Martin; Bison, Brigitte; Kandels, Daniela; Rossius, Anne; Lüttich, Peggy; Baust, Katja; Faulstich-Ritter, Kristin; John, Rainer; Kreisch, Andrea; Landmann, Judyta; Manteufel, Eva; Nest, Alexandra; Prüfe, Jenny; Schubert, Lisa; Stamm, Walther; Timmermann, Beate; Gerss, Joachim; Rutkowski, Stefan; Schlegel, Paul-Gerhardt; Eyrich, Matthias; Gnekow, Astrid K; Frühwald, Michael C; Sönksen, Marthe; Obrecht-Sturm, Denise; Driever, Pablo Hernáiz; Sauerbrey, Axel; Graf, Norbert; Kontny, Udo; Reimann, Christian; Kordes, Uwe; Schwarz, Rudolf; Obser, Tobias; Boschann, Felix; Schüller, Ulrich; Altendorf, Lea; Goschzik, Tobias; Pietsch, Torsten; Mynarek, Martin; Rutkowski, Stefan

Activity of Type II RAF Inhibitor Tovorafenib in a Pediatric Patient With a Recurrent Spindle Cell Sarcoma Harboring a Novel SNX8-BRAF Gene Fusion

II型RAF抑制剂托沃拉非尼在携带新型SNX8-BRAF基因融合的复发性梭形细胞肉瘤患儿中的活性

Offer, Katharine; McGuire, Michael T; Song, Kunchang; Goldfischer, Michael J; Davare, Monika A; Corless, Christopher L; Beadling, Carol; Neff, Tanaya; Cox, Michael C; Govinda Raju, Sandya; Blackman, Samuel C