A novel multiplex RNAi therapy simultaneously targets Hif1a and Hif2a to defy retinal degeneration in two models of AMD
一种新型多重RNAi疗法可同时靶向Hif1a和Hif2a,从而在两种AMD模型中阻止视网膜退化。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.09.044
Ebner, Lynn J A; Imsand, Cornelia; Karademir, Duygu; Peters, Florian; Kiessling, Eva; Fottner, Antonia; Matter, Claudia; Fajardo, Diego S; Merolla, Luca; Wögenstein, Gabriele M; Tsioti, Ioanna; Govers, Larissa P; Blaser, Frank; Meneau, Isabelle; Boye, Sanford L; Boye, Shannon E; Grimm, Christian; Samardzija, Marijana