日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

florio HAEMO-A Digital Medical Device for Monitoring of Treatment, Symptoms and Physical Activities for People Living With Haemophilia

florio HAEMO-A 是一款用于监测血友病患者治疗、症状和身体活动的数字医疗设备

Königs, Christoph; Astermark, Jan; Blatny, Jan; O Hara, Jamie; Iorio, Allfonso; Negrier, Claude; Peyvandi, Flora; Steinitz, Katharina; Reininger, Armin J; Bonanad, Santiago

Atypical Phenotype of Predominant Autoimmune Cytopenia and Impaired Perforin Expression in XMEN Syndrome

XMEN综合征中以自身免疫性血细胞减少症为主的非典型表型和穿孔素表达受损

Grombirikova, Hana; Markocsy, Adam; Kocurkova, Anna; Blatny, Jan; Vlkova, Marcela; Slanina, Peter; Hlavackova, Eva; Fiamoli, Veronika; Schneiderova, Helena; Klocperk, Adam; Ricna, Dita; Fronkova, Eva; Kral, Jan; Salingova, Anna; Jesenak, Milos; Freiberger, Tomas

Congenital fibrinogen disorders: a retrospective clinical and genetic analysis of the Prospective Rare Bleeding Disorders Database

先天性纤维蛋白原疾病:前瞻性罕见出血性疾病数据库的回顾性临床和遗传分析

Mohsenian, Samin; Palla, Roberta; Menegatti, Marzia; Cairo, Andrea; Lecchi, Anna; Casini, Alessandro; Neerman-Arbez, Marguerite; Asselta, Rosanna; Scardo, Sara; Siboni, Simona Maria; Blatny, Jan; Zapletal, Ondrej; Schved, Jean-Francois; Giansily-Blaizot, Muriel; Halimeh, Susan; Daoud, Mohamad Ayman; Platokouki, Helen; Pergantou, Helen; Schutgens, Roger E G; Van Haaften-Spoor, Monique; Brons, Paul; Laros-van Gorkom, Britta; Van Pinxten, Elise; Borhany, Munira; Fatima, Naveena; Mikovic, Danijela; Saracevic, Marko; Özdemir, Gül Nihal; Ay, Yılmaz; Makris, Michael; Lockley, Caryl; Mumford, Andrew; Harvey, Andrew; Austin, Steve; Shapiro, Amy; Williamson, Adrianna; McGuinn, Catherine; Goldberg, Ilene; De Moerloose, Philippe; Peyvandi, Flora

Determinants of bleeding before and during immune tolerance in 222 boys with severe hemophilia A and inhibitors >5 BU

222名患有严重血友病A且抑制因子>5 BU的男孩在免疫耐受前后出血的决定因素

Fischer, Kathelijn; Kenet, Gili; Kurnik, Karin; Carcao, Manuel; Oldenburg, Johannes; Stamm-Mikkelsen, Torben; Cid Haro, Ana Rosa; Koskenvuo, Minna; Blatny, Jan; Königs, Christoph

Analysis of von Willebrand Disease in the "Heart of Europe"

对“欧洲中心地带”血管性血友病的分析

Vangenechten, Inge; Smejkal, Petr; Zavrelova, Jiri; Zapletal, Ondrej; Wild, Alexander; Michiels, Jan Jacques; Berneman, Zwi; Blatny, Jan; Batorova, Angelika; Prigancova, Tatiana; Penka, Miroslav; Gadisseur, Alain

A Practical, One-Clinic Visit Protocol for Pharmacokinetic Profile Generation with the ADVATE myPKFiT Dosing Tool in Severe Hemophilia A Subjects

使用 ADVATE myPKFiT 给药工具在重度血友病 A 患者中生成药代动力学特征的实用单次就诊方案

Blanchette, Victor S; Zunino, Laura; Grassmann, Viviane; Barnes, Chris; Carcao, Manuel D; Curtin, Julie; Jackson, Shannon; Khoo, Liane; Komrska, Vladimir; Lillicrap, David; Morfini, Massimo; Romanova, Gabriela; Stephens, Derek; Zapotocka, Ester; Rand, Margaret L; Blatny, Jan

The prospective Hemophilia Inhibitor PUP Study reveals distinct antibody signatures prior to FVIII inhibitor development

前瞻性血友病抑制剂PUP研究揭示了FVIII抑制剂产生之前的独特抗体特征。

Reipert, B M; Gangadharan, B; Hofbauer, C J; Berg, V; Schweiger, H; Bowen, J; Blatny, J; Fijnvandraat, K; Mullins, E S; Klintman, J; Male, C; McGuinn, C; Meeks, S L; Radulescu, V C; Ragni, M V; Recht, M; Shapiro, A D; Staber, J M; Yaish, H M; Santagostino, E; Brown, D L

Postauthorization safety surveillance study of antihaemophilic factor (recombinant) reconstituted in 2 mL sterile water for injection in children with haemophilia A

抗血友病因子(重组)溶于2 mL注射用无菌水中,用于治疗A型血友病患儿的上市后安全性监测研究

Motwani, Jayashree; Guillet, Benoit; Blatny, Jan; Schilling, Freimut H; Wibaut, Bénédicte; Goldstine, Jimena; Nagy, Andras; Doralt, Jennifer; Engl, Werner; Tangada, Srilatha; Spotts, Gerald

Performing and interpreting individual pharmacokinetic profiles in patients with Hemophilia A or B: Rationale and general considerations

对A型或B型血友病患者进行个体药代动力学分析和解读:原理和一般考虑因素

Iorio, Alfonso; Edginton, Andrea N; Blanchette, Victor; Blatny, Jan; Boban, Ana; Cnossen, Marjon; Collins, Peter; Croteau, Stacy E; Fischer, Katheljin; Hart, Daniel P; Ito, Shinya; Korth-Bradley, Joan; Lethagen, Stefan; Lillicrap, David; Makris, Mike; Mathôt, Ron; Morfini, Massimo; Neufeld, Ellis J; Spears, Jeffrey

L-alanine-induced germination in Bacillus licheniformis -the impact of native gerA sequences.

L-丙氨酸诱导地衣芽孢杆菌萌发——天然gerA序列的影响

Madslien Elisabeth H, Granum Per Einar, Blatny Janet M, Lindbäck Toril