Improving angiogenesis ameliorates the efficacy of ASO-based exon skipping for the treatment of Duchenne muscular dystrophy.
改善血管生成可提高基于 ASO 的外显子跳跃治疗杜氏肌营养不良症的疗效。
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2026.102834
Blitek Mathilde, Gastaldi Cécile, Doisy Mathilde, Le Coz Olivier, David Marion, Phongsavanh Xaysongkhame, Ben Aicha Sameh, Garcia Luis, Rotini Alessio, Pagès Gilles, Goyenvalle Aurélie