日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Dilated Cardiomyopathy and Later Onset Limb-Girdle Muscular Dystrophy Associated With Fukutin and LaminA/C Mutations

与福库汀和层粘蛋白A/C突变相关的扩张型心肌病和晚发型肢带型肌营养不良症

Cardona Perez, Alejandra; Moenning, Renee; Bodkin, Cynthia; Gutmann, Laurie; Helm, Benjamin M; Wells, Layne; Moore, Steven A; Ilonze, Onyedika J

Multicenter Expanded Access Protocol for Research Through Access to Trehalose in People With Amyotrophic Lateral Sclerosis

通过获取海藻糖,为肌萎缩侧索硬化症患者开展研究的多中心扩大使用方案

Krivickas, Brooke; Scirocco, Erica; Giacomelli, Elisa; Sharma, Saloni; Benson, Molly; Keegan, Mackenzie; Kulesa-Kelley, Jennifer; Chibnik, Lori B; Casagrande, Gabriella; Heyd, Lindsay; Chase, Marianne; Drake, Kristin; Mohapatra, Silpa; Hagar, Jennifer Linn; Hasenoehrl, Meredith Gibbons; Dagostino, Derek; Sherman, Alexander V; Leite, Alex; Yu, Hong; Rosenthal, Jesse; Miller, Timothy; McCaffrey, Alexandra; Gwathmey, Kelly; Locatelli, Eduardo; Bayat, Elham; Heitzman, Daragh; Young, Eufrosina; Goyal, Namita A; Whitesell, Jackie; Felice, Kevin; Ilieva, Hristelina; Swenson, Andrea; Walk, David; Alameda, Gustavo; Foster, Laura; McIlduff, Courtney E; Walsh, Alison; Zilliox, Lindsay; Ajroud-Driss, Senda; Bodkin, Cynthia; Katz, Jonathan; Ladha, Shafeeq; Rivner, Michael; Rosow, Laura; Twydell, Paul; Wasiewski, Warren; Babu, Suma; Berry, James D; Paganoni, Sabrina

Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial.

替戈普鲁巴特治疗肌萎缩侧索硬化症患者的安全性和耐受性:一项 2A 期临床试验

Perrin Steven, Ladha Shafeeq, Maragakis Nicholas, Rivner Michael H, Katz Jonathan, Genge Angela, Olney Nicholas, Lange Dale, Heitzman Daragh, Bodkin Cynthia, Jawdat Omar, Goyal Namita A, Bornstein Jeffrey D, Mak Carmen, Appel Stanley H, Paganoni Sabrina

Randomized phase 2 study of ACE-083, a muscle-promoting agent, in facioscapulohumeral muscular dystrophy

ACE-083(一种肌肉促进剂)治疗面肩肱型肌营养不良症的随机二期研究

Statland, Jeffrey M; Campbell, Craig; Desai, Urvi; Karam, Chafic; Díaz-Manera, Jordi; Guptill, Jeffrey T; Korngut, Lawrence; Genge, Angela; Tawil, Rabi N; Elman, Lauren; Joyce, Nanette C; Wagner, Kathryn R; Manousakis, Georgios; Amato, Anthony A; Butterfield, Russell J; Shieh, Perry B; Wicklund, Matthew; Gamez, Josep; Bodkin, Cynthia; Pestronk, Alan; Weihl, Conrad C; Vilchez-Padilla, Juan J; Johnson, Nicholas E; Mathews, Katherine D; Miller, Barry; Leneus, Ashley; Fowler, Marcie; van de Rijn, Marc; Attie, Kenneth M

Myasthenia Gravis and Lambert-Eaton Myasthenic Syndrome: New Developments in Diagnosis and Treatment

重症肌无力和兰伯特-伊顿肌无力综合征:诊断和治疗的新进展

Pascuzzi, Robert M; Bodkin, Cynthia L

A Phase 2, Double-Blind, Randomized, Dose-Ranging Trial Of Reldesemtiv In Patients With ALS

一项针对肌萎缩侧索硬化症(ALS)患者的瑞德西姆替夫(Reldesemtiv)II期双盲随机剂量范围试验。

Shefner, Jeremy M; Andrews, Jinsy A; Genge, Angela; Jackson, Carlayne; Lechtzin, Noah; Miller, Timothy M; Cockroft, Bettina M; Meng, Lisa; Wei, Jenny; Wolff, Andrew A; Malik, Fady I; Bodkin, Cynthia; Brooks, Benjamin R; Caress, James; Dionne, Annie; Fee, Dominic; Goutman, Stephen A; Goyal, Namita A; Hardiman, Orla; Hayat, Ghazala; Heiman-Patterson, Terry; Heitzman, Daragh; Henderson, Robert D; Johnston, Wendy; Karam, Chafic; Kiernan, Matthew C; Kolb, Stephen J; Korngut, Lawrence; Ladha, Shafeeq; Matte, Genevieve; Mora, Jesus S; Needham, Merrilee; Oskarsson, Bjorn; Pattee, Gary L; Pioro, Erik P; Pulley, Michael; Quan, Dianna; Rezania, Kourosh; Schellenberg, Kerri L; Schultz, David; Shoesmith, Christen; Simmons, Zachary; Statland, Jeffrey; Sultan, Shumaila; Swenson, Andrea; Berg, Leonard H Van Den; Vu, Tuan; Vucic, Steve; Weiss, Michael; Whyte-Rayson, Ashley; Wymer, James; Zinman, Lorne; Rudnicki, Stacy A

GABA and glutamate levels in occlusal splint-wearing males with possible bruxism

佩戴咬合夹板且可能患有磨牙症的男性患者的 GABA 和谷氨酸水平

Dharmadhikari, Shalmali; Romito, Laura M; Dzemidzic, Mario; Dydak, Ulrike; Xu, Jun; Bodkin, Cynthia L; Manchanda, Shalini; Byrd, Kenneth E