Uncoupling N-acetylaspartate from brain pathology: implications for Canavan disease gene therapy
将N-乙酰天冬氨酸与脑部病理学解耦:对卡纳万病基因治疗的意义
期刊:Acta Neuropathologica
影响因子:9.3
doi:10.1007/s00401-017-1784-9
von Jonquieres, Georg; Spencer, Ziggy H T; Rowlands, Benjamin D; Klugmann, Claudia B; Bongers, Andre; Harasta, Anne E; Parley, Kristina E; Cederholm, Jennie; Teahan, Orla; Pickford, Russell; Delerue, Fabien; Ittner, Lars M; Fröhlich, Dominik; McLean, Catriona A; Don, Anthony S; Schneider, Miriam; Housley, Gary D; Rae, Caroline D; Klugmann, Matthias