Skeletal muscle effects of antisense oligonucleotides targeting glycogen synthase 1 in a mouse model of Pompe disease.
针对庞贝氏病小鼠模型中糖原合成酶 1 的反义寡核苷酸对骨骼肌的影响
期刊:Clinical and Translational Medicine
影响因子:6.8
doi:10.1002/ctm2.70314
Weiss Lan, Carrer Michele, Shmara Alyaa, Martin Angela, Yin Hong, Pal Pallabi, Cheng Cheng, Ta Lac, Boock Victoria, Fazeli Yasamin, Chang Mindy, Paguio Marvin, Lee Jonathan, Yu Howard, Weiss John, Grossman Tamar R, Raben Nina, Jafar-Nejad Paymaan, Kimonis Virginia
