AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype
利用AAV介导的CRB1患者来源视网膜类器官基因增强疗法可恢复视网膜的组织学和转录表型
期刊:Stem Cell Reports
影响因子:5.1
doi:10.1016/j.stemcr.2023.05.008
Boon, Nanda; Lu, Xuefei; Andriessen, Charlotte A; Moustakas, Ioannis; Buck, Thilo M; Freund, Christian; Arendzen, Christiaan H; Böhringer, Stefan; Boon, Camiel J F; Mei, Hailiang; Wijnholds, Jan
