Minimal Essential Human Factor VIII Alterations Enhance Secretion and Gene Therapy Efficiency
最小必需人凝血因子VIII改变可增强分泌和基因治疗效率
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2020.10.013
Cao, Wenjing; Dong, Biao; Horling, Franziska; Firrman, Jenni A; Lengler, Johannes; Klugmann, Matthias; de la Rosa, Maurus; Wu, Wenman; Wang, Qizhao; Wei, Hongying; Moore, Andrea R; Roberts, Sean A; Booth, Carmen J; Hoellriegl, Werner; Li, Dong; Konkle, Barbara; Miao, Carol; Reipert, Birgit M; Scheiflinger, Friedrich; Rottensteiner, Hanspeter; Xiao, Weidong