RNA base editing therapy cures hearing loss induced by OTOF gene mutation
RNA碱基编辑疗法治愈OTOF基因突变引起的听力损失
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2023.10.019
Yuanyuan Xue, Yong Tao, Xing Wang, Xueling Wang, Yilai Shu, Yuanhua Liu, Wen Kang, Sifan Chen, Zhenzhe Cheng, Boou Yan, Yanwei Xie, Lanting Bi, Haitao Jia, Jinhui Li, Qingquan Xiao, Liying Chen, Xuan Yao, Linyu Shi, Hui Yang, Hao Wu