CRISPR/Cas9 gene therapy increases the risk of tumorigenesis in the mouse model of hereditary tyrosinemia type I.
CRISPR/Cas9 基因疗法增加了 I 型遗传性酪氨酸血症小鼠模型发生肿瘤的风险
期刊:Jhep Reports
影响因子:7.5
doi:10.1016/j.jhepr.2025.101327
Chen Tong, Barzi Mercedes, Furey Nika, Kim Hyunjae R, Pankowicz Francis P, Legras Xavier, Elsea Sara H, Hurley Ayrea E, Yang Diane, Wheeler David A, Borowiak Malgorzata, Bissig-Choisat Beatrice, Sumazin Pavel, Bissig Karl-Dimiter