日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A humanized anaplastic lymphoma kinase (ALK)-directed antibody-drug conjugate with pyrrolobenzodiazepine payload demonstrates efficacy in ALK-expressing cancers.

一种以吡咯并苯二氮卓类药物为有效载荷的人源化间变性淋巴瘤激酶(ALK)靶向抗体药物偶联物,在表达ALK的癌症中显示出疗效

Guerra Alberto D, Matkar Smita, Acholla Christina, Casey Colleen, Li Grant, Mazzeschi Martina, Patel Khushbu, Krytska Kateryna, Chen Chuan, Balyasny Skye, Kalna Joshua, Kamitsuka Paul, Gerelus Mark, Polkosnik Grace, Groff David, Mukherje Apratim, Adams Cynthia, Witek Gabriela, Hamilton Amber K, Martinez Daniel, Pogoriler Jennifer, Spear Timothy T, Li Yimei, Jung Piotr, Alvarado Diego, Lauriola Mattia, Maris John M, Wolpaw Adam J, Bosse Kristopher R, Dimitrov Dimiter, Mir Mustafa, Jelev Dontcho V, Mossé Yael P

Target antigen-displaying extracellular vesicles boost CAR T cell efficacy in cell and mouse models of neuroblastoma

靶向抗原展示的细胞外囊泡可增强CAR-T细胞在神经母细胞瘤细胞和鼠模型中的疗效

Giudice, Anna Maria; Matlaga, Stephanie; Roth, Sydney L; Pascual-Pasto, Guillem; Schürch, Patrick M; Rouin, Geoffrey; McIntyre, Brendan; Grothusen, Grant P; Cresswell-Clay, Evan; Shraim, Rawan; Groff, David; Zecchino, Vincent; Lombardi, Simona; Martinez, Daniel; Spruce, Lynn A; Brown, Elizabeth M; Fazelinia, Hossein; Henrickson, Sarah E; Nance, Jonas; Reynolds, C Patrick; Bosse, Kristopher R

D3-GPC2-Directed CAR T Cells Are Safe and Efficacious in Preclinical Models of Neuroblastoma and Small Cell Lung Cancer.

D3-GPC2 靶向 CAR T 细胞在神经母细胞瘤和小细胞肺癌的临床前模型中安全有效。

Giudice Anna Maria, Matlaga Stephanie, Roth Sydney L, Gladney Whitney, Groff David, Hofmann Ted J, McDaid Kendra S, Pascual-Pasto Guillem, McIntyre Brendan, Zecchino Vincent, Martinez Dan, Spear Timothy T, Wolpaw Adam J, Assenmacher Charles-Antoine, Radaelli Enrico, Pogoriler Jenny, Pawel Bruce, Barrett David, Grupp Stephan A, Maris John M, Bosse Kristopher R

Blocking MIF secretion enhances CAR T-cell efficacy against neuroblastoma.

抑制MIF分泌可增强CAR T细胞对神经母细胞瘤的疗效

Strijker Josephine G M, Pascual-Pasto Guillem, Grothusen Grant P, Kalmeijer Yannine J, Kalaitsidou Elisavet, Zhao Chunlong, McIntyre Brendan, Matlaga Stephanie, Visser Lindy L, Barisa Marta, Himsworth Courtney, Shah Rivani, Muller Henrike, Schild Linda G, Hains Peter G, Zhong Qing, Reddel Roger R, Robinson Phillip J, Catena Xavier, Soengas María S, Margaritis Thanasis, Dekker Frank J, Anderson John, Molenaar Jan J, Bosse Kristopher R, Wu Wei, Wienke Judith

Scratching the surface of targeting GPC2 on pediatric CNS tumors

靶向GPC2治疗儿童中枢神经系统肿瘤的初步研究

Pan, Hehai; Foster, Jessica B; Bosse, Kristopher R

A proteogenomic surfaceome study identifies DLK1 as an immunotherapeutic target in neuroblastoma.

蛋白质基因组表面组学研究发现 DLK1 是神经母细胞瘤的免疫治疗靶点

Hamilton Amber K, Radaoui Alexander B, Tsang Matthew, Martinez Daniel, Conkrite Karina L, Patel Khushbu, Sidoli Simone, Delaidelli Alberto, Modi Apexa, Rokita Jo Lynne, Lane Maria V, Hartnett Nicholas, Lopez Raphael D, Zhang Bo, Zhong Chuwei, Ennis Brian, Miller Daniel P, Brown Miguel A, Rathi Komal S, Raman Pichai, Pogoriler Jennifer, Bhatti Tricia, Pawel Bruce, Glisovic-Aplenc Tina, Teicher Beverly, Erickson Stephen W, Earley Eric J, Bosse Kristopher R, Sorensen Poul H, Krytska Kateryna, Mosse Yael P, Havenith Karin E, Zammarchi Francesca, van Berkel Patrick H, Smith Malcolm A, Garcia Benjamin A, Maris John M, Diskin Sharon J

Germline pathogenic variants in neuroblastoma patients are enriched in BARD1 and predict worse survival

神经母细胞瘤患者的种系致病变异富集于BARD1基因,并预示着更差的生存期。

Kim, Jung; Vaksman, Zalman; Egolf, Laura E; Kaufman, Rebecca; Evans, J Perry; Conkrite, Karina L; Danesh, Arnavaz; Lopez, Gonzalo; Randall, Michael P; Dent, Maiah H; Farra, Lance M; Menghani, Neil L; Dymek, Malwina; Desai, Heena; Hausler, Ryan; Hicks, Belynda; Guidry Auvil, Jaime; Gerhard, Daniela S; Hakonarson, Hakon; Maxwell, Kara N; Cole, Kristina A; Pugh, Trevor J; Bosse, Kristopher R; Khan, Javed; Wei, Jun S; Maris, John M; Stewart, Douglas R; Diskin, Sharon J

Retraction Note: Cross-HLA targeting of intracellular oncoproteins with peptide-centric CARs

撤稿声明:利用肽中心CAR靶向细胞内癌蛋白的跨HLA

Yarmarkovich, Mark; Marshall, Quinlen F; Warrington, John M; Premaratne, Rasika; Farrel, Alvin; Groff, David; Li, Wei; di Marco, Moreno; Runbeck, Erin; Truong, Hau; Toor, Jugmohit S; Tripathi, Sarvind; Nguyen, Son; Shen, Helena; Noel, Tiffany; Church, Nicole L; Weiner, Amber; Kendsersky, Nathan; Martinez, Dan; Weisberg, Rebecca; Christie, Molly; Eisenlohr, Laurence; Bosse, Kristopher R; Dimitrov, Dimiter S; Stevanovic, Stefan; Sgourakis, Nikolaos G; Kiefel, Ben R; Maris, John M

Germline pathogenic variants in 786 neuroblastoma patients

786例神经母细胞瘤患者的种系致病变异

Kim, Jung; Vaksman, Zalman; Egolf, Laura E; Kaufman, Rebecca; Evans, J Perry; Conkrite, Karina L; Danesh, Arnavaz; Lopez, Gonzalo; Randall, Michael P; Dent, Maiah H; Farra, Lance M; Menghani, Neil; Dymek, Malwina; Desai, Heena; Hausler, Ryan; Guidry Auvil, Jaime M; Gerhard, Daniela S; Hakonarson, Hakon; Maxwell, Kara N; Cole, Kristina A; Pugh, Trevor J; Bosse, Kristopher R; Khan, Javed; Wei, Jun S; Maris, John M; Stewart, Douglas R; Diskin, Sharon J

Development of GPC2-directed chimeric antigen receptors using mRNA for pediatric brain tumors

利用mRNA开发GPC2靶向嵌合抗原受体治疗儿童脑肿瘤

Foster, Jessica B; Griffin, Crystal; Rokita, Jo Lynne; Stern, Allison; Brimley, Cameron; Rathi, Komal; Lane, Maria V; Buongervino, Samantha N; Smith, Tiffany; Madsen, Peter J; Martinez, Daniel; Delaidelli, Alberto; Sorensen, Poul H; Wechsler-Reya, Robert J; Karikó, Katalin; Storm, Phillip B; Barrett, David M; Resnick, Adam C; Maris, John M; Bosse, Kristopher R