An AAV capsid reprogrammed to bind human Transferrin Receptor mediates brain-wide gene delivery
重新编程以结合人类转铁蛋白受体的 AAV 衣壳介导全脑基因传递
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doi:10.1101/2023.12.20.572615
Qin Huang, Ken Y Chan, Shan Lou, Casey Keyes, Jason Wu, Nuria R Botticello-Romero, Qingxia Zheng, Jencilin Johnston, Allan Mills, Pamela P Brauer, Gabrielle Clouse, Simon Pacouret, John W Harvey, Thomas Beddow, Jenna K Hurley, Isabelle G Tobey, Megan Powell, Albert T Chen, Andrew J Barry, Fatma-Elza