日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

RNA editing for the treatment of alpha-1 antitrypsin deficiency.

RNA 编辑用于治疗 α-1 抗胰蛋白酶缺乏症。

Monian Prashant, Shivalila Chikdu, Lu Genliang, Bowman Keith, Briem Stearne, Bylsma Marissa, Byrne Michael, Cannon Megan, Chatterjee Arindom, Dallaire Morgan, Desai Jigar, Dufresne Jason, Faraone Alyse, Favaloro Frank, Friend Stephen, Ghosh Anamitra, Godfrey Jack, Hernandez Nidia, Huth Olivia, Iwamoto Naoki, Kawamoto Tomomi, Lamattina Anthony, Lemaitre Muriel, Lindsey Amber, Liu Fangjun, Looby Richard, Luu Khoa, McGlynn Andrew, Metterville Jake, Paik Ik-Hyeon, Pan Qianli, Patil Saurabh, Pu Tom, Purcell-Estabrook Erin, Ranade Ashwini, Rheinhardt Jeanette, Rossi Jeff, Shimizu Mamoru, Singh Kuldeep, Standley Stephany, Thomas Carina, Tripathi Snehlata, Yang Hailin, Yordanoff Ryan, Yin Yuan, Yu Hui, Narayanan PadmaKumar, Kandasamy Pachamuthu, Giangrande Paloma H, Vargeese Chandra

Castrate-resistant prostate cancer response to taxane is determined by an HNF1-dependent apoptosis resistance circuit

去势抵抗性前列腺癌对紫杉烷类药物的反应取决于HNF1依赖性细胞凋亡抵抗回路。

Ilya S Senatorov,Joel Bowman,Keith H Jansson,Aian Neil Alilin,Brian J Capaldo,Ross Lake,Morgan Riba,Yasmine C Abbey,Crystal Mcknight,Xiaohu Zhang,Sonam Raj,Michael L Beshiri,Paul Shinn,Holly Nguyen,Craig J Thomas,Eva Corey,Kathleen Kelly

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

对立体纯反义寡核苷酸进行临床前评估,以选择性降低突变型HTT的表达水平。

Iwamoto, Naoki; Liu, Yuanjing; Frank-Kamenetsky, Maria; Maguire, Abbie; Tseng, Wei Chou; Taborn, Kristin; Kothari, Nayantara; Akhtar, Ali; Bowman, Keith; Shelke, Juili Dilip; Lamattina, Anthony; Hu, Xiao Shelley; Jang, Hyun Gyung; Kandasamy, Pachamuthu; Liu, Fangjun; Longo, Ken; Looby, Richard; Meena; Metterville, Jake; Pan, Qianli; Purcell-Estabrook, Erin; Shimizu, Mamoru; Prakasha, Priyanka Shiva; Standley, Stephany; Upadhyay, Hansini; Yang, Hailin; Yin, Yuan; Zhao, Anderson; Francis, Christopher; Byrne, Mike; Dale, Elena; Verdine, Gregory L; Vargeese, Chandra

Stereochemistry Enhances Potency, Efficacy, and Durability of Malat1 Antisense Oligonucleotides In Vitro and In Vivo in Multiple Species

立体化学增强了Malat1反义寡核苷酸在体外和体内多种物种中的效力、功效和持久性

Byrne, Michael; Vathipadiekal, Vinod; Apponi, Luciano; Iwamoto, Naoki; Kandasamy, Pachamuthu; Longo, Kenneth; Liu, Fangjun; Looby, Richard; Norwood, Lauren; Shah, Anee; Shelke, Juili Dilip; Shivalila, Chikdu; Yang, Hailin; Yin, Yuan; Guo, Lankai; Bowman, Keith; Vargeese, Chandra

Genomic discovery of an evolutionarily programmed modality for small-molecule targeting of an intractable protein surface

基因组学发现一种进化编程模式,用于小分子靶向难以处理的蛋白质表面

Uddhav K Shigdel, Seung-Joo Lee, Mathew E Sowa, Brian R Bowman, Keith Robison, Minyun Zhou, Khian Hong Pua, Dylan T Stiles, Joshua A V Blodgett, Daniel W Udwary, Andrew T Rajczewski, Alan S Mann, Siavash Mostafavi, Tara Hardy, Sukrat Arya, Zhigang Weng, Michelle Stewart, Kyle Kenyon, Jay P Morgenste

Effect of Porosity on Strength Distribution of Microcrystalline Cellulose

孔隙率对微晶纤维素强度分布的影响

Keleṣ, Özgür; Barcenas, Nicholas P; Sprys, Daniel H; Bowman, Keith J