Identification of NUV-244 as a PNPLA3 I148M degrading small molecule.
鉴定 NUV-244 为 PNPLA3 I148M 降解小分子
期刊:iScience
影响因子:4.1
doi:10.1016/j.isci.2025.112384
Steigemann Patrick, Braeuer Nico, Puetter Vera, Zablowsky Nina, Juenemann Katrin, von Nussbaum Franz, Lesche Ralf, Dittmar Nicole, Schaller David, Makowska Zuzanna, Klironomos Filippos, Schwarz Susanne, Launhardt Daniela, Bader Benjamin, Lange Martin, Steuber Holger, Black Mary Helen, Packer Jonathan S, Romeo Stefano, Fasler Stephan, Bedford Lisa, Dewey Frederick E