Haploinsufficiency leads to neurodegeneration in C9ORF72 ALS/FTD human induced motor neurons
单倍体不足导致 C9ORF72 ALS/FTD 人类诱发运动神经元发生神经退化
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/nm.4490
Yingxiao Shi, Shaoyu Lin, Kim A Staats, Yichen Li, Wen-Hsuan Chang, Shu-Ting Hung, Eric Hendricks, Gabriel R Linares, Yaoming Wang, Esther Y Son, Xinmei Wen, Kassandra Kisler, Brent Wilkinson, Louise Menendez, Tohru Sugawara, Phillip Woolwine, Mickey Huang, Michael J Cowan, Brandon Ge, Nicole Koutso