Impact of pre-existing immunity on safety and biodistribution of a single AAV9 vectorintrathecal injection in cynomolgus monkeys.
既往免疫对食蟹猴单次鞘内注射 AAV9 载体的安全性和生物分布的影响。
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101602
Vono Maria, Rio Tony Del, Magdaleno Eduardo, Loll Nathalie R, Jarvis Philip, Walter Catherine, Kikkawa Rie, Mansfield Keith, McBlane Fraser, Sirivelu Madhu P, Ozsolak Fatih, Brees Dominique, Hudry Eloise, Rubic-Schneider Tina, Tukov Francis Fonyuy, Huang Guanrong