Real-world evidence in achondroplasia: considerations for a standardized data set
软骨发育不全的真实世界证据:标准化数据集的考量
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-023-02755-w
Alanay, Yasemin; Mohnike, Klaus; Nilsson, Ola; Alves, Inês; AlSayed, Moeenaldeen; Appelman-Dijkstra, Natasha M; Baujat, Genevieve; Ben-Omran, Tawfeg; Breyer, Sandra; Cormier-Daire, Valerie; Gregersen, Pernille Axél; Guillén-Navarro, Encarna; Högler, Wolfgang; Maghnie, Mohamad; Mukherjee, Swati; Cohen, Shelda; Pimenta, Jeanne; Selicorni, Angelo; Semler, J Oliver; Sigaudy, Sabine; Popkov, Dmitry; Sabir, Ian; Noval, Susana; Sessa, Marco; Irving, Melita