GM1 Gangliosidosis Type II: Results of a 10-Year Prospective Study
GM1神经节苷脂沉积症II型:一项为期10年的前瞻性研究结果
期刊:
影响因子:
doi:10.1101/2024.01.04.24300778
D'Souza, Precilla; Farmer, Cristan; Johnston, Jean; Han, Sangwoo T; Adams, David; Hartman, Adam L; Zein, Wadih; Huryn, Laryssa A; Solomon, Beth; King, Kelly; Jordan, Christopher; Myles, Jennifer; Nicoli, Elena-Raluca; Rothermel, Caroline E; Algarin, Yoliann Mojica; Huang, Reyna; Quimby, Rachel; Zainab, Mosufa; Bowden, Sarah; Crowell, Anna; Buckley, Ashura; Brewer, Carmen; Regier, Deborah; Brooks, Brian; Baker, Eva; Vézina, Gilbert; Thurm, Audrey; Tifft, Cynthia J