日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

SUN-644 Pharmacological Approaches in Lipodystrophy: Concomitant Medication and Metreleptin Therapy Use in the Participants of LD-Lync Study

SUN-644 脂肪营养不良的药理学方法:LD-Lync 研究参与者中伴随用药和米曲普汀治疗的使用

Du, Shicong; Lin, Huiju; Luo, Qiong; Man, Chung Ling; Lai, Sze Han; Ho, Kin Fai; Leung, Kenneth M Y; Lee, Patrick K H; Guler, Merve Celik; Besci, Ozge; Foss de Freitas, Maria Cristina; Yosef, Matheos; Khalatbari, Shoukoufeh; Ashmus, Michelle; Guler, Demircan; Gilio, Donatella; Kaba, Diarratou; Uwandu, Chika Divine; Gomes, Anabela Dill; Tuska, Rebecca; Brush, Maiah; Hwang, Michael; Neal, Trinity; Tracey, Britney; Okawa, Marinna; Brite, Brianna; Richison, Carman; Simsir, Ilgin Yildirim; Akinci, Baris; Brown, Rebecca J; Oral, Elif A; Guler, Merve Celik; Foss de Freitas, Maria Cristina; Yosef, Matheos; Khalatbari, Shoukoufeh; Ashmus, Michelle; Guler, Demircan; Gilio, Donatella; Kaba, Diarratou; Gomes, Anabela Dill; Uwandu, Chika Divine; Brush, Maiah; Tuska, Rebecca; Neal, Trinity; Hwang, Michael; Tracey, Britney; Okawa, Marinna; Brite, Brianna; Richison, Carman; Simsir, Ilgin Yildirim; Akinci, Baris; Brown, Rebecca J; Oral, Elif A

Volanesorsen, an antisense oligonucleotide to apolipoprotein C-III, increases lipoprotein lipase activity and lowers triglycerides in partial lipodystrophy.

Volanesorsen 是一种针对载脂蛋白 C-III 的反义寡核苷酸,可增加脂蛋白脂肪酶活性,降低部分脂肪营养不良患者的甘油三酯水平

Lightbourne Marissa, Startzell Megan, Bruce Kimberley D, Brite Brianna, Muniyappa Ranganath, Skarulis Monica, Shamburek Robert, Gharib Ahmed M, Ouwerkerk Ronald, Walter Mary, Eckel Robert H, Brown Rebecca J