日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Simtuzumab Attenuates Loxl2-Mediated Extracellular Matrix Remodeling and Preserves Cardiac Function in LMNA Mutation-Induced Dilated Cardiomyopathy

Simtuzumab 可减轻 Loxl2 介导的细胞外基质重塑,并在 LMNA 突变诱发的扩张型心肌病中维持心脏功能。

Kervella, Marie; Behrens, Charlotta S; Peccate, Cécile; Guesmia, Zoheir; Grandi, Fiorella; Mougenot, Nathalie; Forand, Anne; Charrabi, Azzouz; Brochier, Guy; Andriantsitohaina, Ramaroson; Singh, Sonia R; Eschenhagen, Thomas; Meli, Albano C; Muchir, Antoine

Disease exacerbation in human DMD MYOrganoids enables gene therapy evaluation and unveils persistence of fibrotic activity

人类杜氏肌营养不良症(DMD)肌类器官疾病加重可评估基因治疗效果,并揭示纤维化活动的持续存在

Palmieri, Laura; Bimbi, Giorgia; Ferrand, Maxime; Marcello, Matteo; Pili, Louna; Hong, Ai Vu; Jaber, Abbass; El-Khoury, Riyad; Brochier, Guy; Bigot, Anne; Israeli, David; Richard, Isabelle; Albini, Sonia

Author Correction: Disease exacerbation in human DMD MYOrganoids enables gene therapy evaluation and unveils persistence of fibrotic activity

作者更正:人类DMD MYOrganoids中的疾病加剧可实现基因治疗评估并揭示纤维化活动的持续存在

Palmieri, Laura; Bimbi, Giorgia; Ferrand, Maxime; Marcello, Matteo; Pili, Louna; Hong, Ai Vu; Jaber, Abbass; El-Khoury, Riyad; Brochier, Guy; Bigot, Anne; Israeli, David; Richard, Isabelle; Albini, Sonia

Clinical, morphological, and molecular characterization of patients with X-linked myopathy with excessive autophagy (XMEA).

对患有过度自噬的 X 连锁肌病 (XMEA) 的患者进行临床、形态学和分子特征分析。

Merlet Angèle N, Lacène Emmanuelle, Nelson Isabelle, Brochier Guy, Labasse Clémence, Chanut Anais, Madelaine Angeline, Beuvin Maud, Bonne Gisèle, Féasson Léonard, Minot Marie-Christine, Noury Jean-Baptiste, Fradin Mélanie, Savarese Marco, Fernández-Eulate Gorka, Behin Anthony, Stojkovic Tanya, Hentschel Andreas, Marcorelles Pascale, Roos Andreas, Evangelista Teresinha

Voice identity invariance by anterior temporal lobe neurons

前颞叶神经元对声音身份不变性的调控

Giamundo, Margherita; Trapeau, Régis; Thoret, Etienne; Renaud, Luc; Brochier, Thomas; Belin, Pascal

Disease spectrum and long-term prognosis of patients with BAG3-associated neuromuscular diseases in Europe

欧洲BAG3相关神经肌肉疾病患者的疾病谱和长期预后

Fernández-Eulate, Gorka; Gitiaux, Cyril; Thiele, Simone; Jungbluth, Heinz; Potulska-Chromik, Anna; Marini-Bettolo, Chiara; Davion, Jean Baptiste; Morís, Germán; Gallardo, Eduard; Olivé, Montse; de Fuenmayor-Fernández de la Hoz, Carlos Pablo; Audic, Frederique; Isapof, Arnaud; Walter, Maggie C; Angelini, Corrado; Bertini, Enrico; Schara-Schmidt, Ulrike; Claeys, Kristl G; Dohrn, Maike F; Dembele, Mohamed; Fer, Frédéric; Brochier, Guy; Evangelista, Teresinha; Kostera-Pruszczyk, Anna; Attarian, Shahram; Straub, Volker; Domínguez-González, Cristina; Vissing, John; Richard, Pascale; Metay, Corinne; Khraiche, Diala; Wahbi, Karim; Stojkovic, Tanya

Consistent clinical factor VIII equivalency is unlikely for non-factor therapies in hemophilic mice

在血友病小鼠中,非因子疗法不太可能达到一致的临床因子VIII等效疗效。

Sefiane, Thibaud; McCluskey, Geneviève; Clavel, Marie; Maynadié, Hortense; Peyron, Ivan; David, Tovo; Brochier, Camille; Saller, François; Khamari, Mariem; Denis, Cécile V; Christophe, Olivier D; Lenting, Peter J; Muczynski, Vincent; Casari, Caterina

Erratum to: "Consistent clinical factor VIII equivalency is unlikely for non-factor therapies in hemophilic mice"

更正:“对于血友病小鼠的非因子疗法而言,不太可能出现一致的临床因子VIII等效性”

Sefiane, Thibaud; McCluskey, Geneviève; Clavel, Marie; Maynadié, Hortense; Peyron, Ivan; David, Tovo; Brochier, Camille; Saller, François; Khamari, Mariem; Denis, Cécile V; Christophe, Olivier D; Lenting, Peter J; Muczynski, Vincent; Casari, Caterina

Detection of spontaneous anti-neoepitope T-cell responses in non-metastatic bladder cancer patients

检测非转移性膀胱癌患者体内自发性抗新表位T细胞反应

Brochier, Walther; Nguyen, Sylvain; Cesson, Valérie; Bricard, Orian; van Baren, Nicolas; Hames, Gérald; Dauguet, Nicolas; Dano, Hélène; Tombal, Bertrand; Rodrigues-Dias, Sonia-Cristina; Masnada, Audrey; Genolet, Raphael; Harari, Alexandre; Roth, Beat; Lucca, Ilaria; Nardelli-Haefliger, Denise; Coulie, Pierre G; Derré, Laurent

Genomic characterisation of novel extremophile lineages from the thalassohaline lake Dziani Dzaha expands the metabolic repertoire of the PVC superphylum

对来自海水湖泊 Dziani Dzaha 的新型极端微生物谱系的基因组表征扩展了 PVC 超门的代谢谱系

Vigneron, Adrien; Cloarec, Lilian A; Brochier-Armanet, Céline; Flandrois, Jean Pierre; Troussellier, Marc; Bernard, Cécile; Agogué, Hélène; Oger, Philippe M; Hugoni, Mylène