Large deletions in the F8 gene predict immune tolerance induction failure in people with severe hemophilia A
F8基因的大片段缺失预示着重度A型血友病患者免疫耐受诱导失败。
期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.103212
Oomen, Ilja; Abdi, Amal; Broer, Linda; Camelo, Ricardo M; Callado, Fábia M R A; Carvalho, Luany E M; Calcaterra, Ilenia L; Carcao, Manuel; Castaman, Giancarlo; Eikenboom, Jeroen C J; Fischer, Kathelijn; Franco, Vivian K B; Geissler, Judy; Kuijpers, Taco W; Leebeek, Frank W G; Lillicrap, David; Lorenzato, Cláudia S; Mancuso, Maria Elisa; Matino, Davide; Di Minno, Matteo N D; Mo, Aomei; Mohseny, Alex B; Nagelkerke, Sietse Q; Oldenburg, Johannes; Rezende, Suely Meireles; Rivard, Georges-Etienne; Rydz, Natalia; Schols, Saskia E M; Tanck, Michael W T; Voorberg, Jan; Fijnvandraat, Karin; Gouw, Samantha C